Results 171 to 173 of about 2,159 (173)

Comparing the effectiveness of gene therapies for pediatric spinal muscular atrophy: Zolgensma, spinraza, and risdiplam

Journal of the Neurological Sciences
Jaimin Rathod, Maneet Kaur, Komati Sathwika, Tejsharani Beeram, Zeel Patel, Srijamya Na   +5 more
openaire   +1 more source

Zolgensma - one-time gene therapy for spinal muscular atrophy.

The Medical letter on drugs and therapeutics, 2019
openaire   +1 more source

Health ministers condemn Novartis lottery for Zolgensma, the world’s most expensive drug

BMJ, The
exaly