Results 241 to 250 of about 1,349,968 (301)

Data-driven springback prediction of curved metal sections in curtain wall systems. [PDF]

Sci Rep
Jiang W, Zhang Y, Liang Y, Chen K.
europepmc   +1 more source

Onasemnogene Abeparvovec in Type I Spinal Muscular Atrophy: 24‐Month Follow‐Up From the Italian Registry

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Onasemnogene abeparvovec (OA) is an AAV9‐based gene therapy for spinal muscular atrophy type I (SMA I). Real‐world outcomes show increased response variability compared to clinical trials, and follow‐up data beyond 12–18 months are limited.
Marika Pane, Giorgia Coratti, Chiara Cutrì, Antonio Varone, Riccardo Masson, Adele D'Amico, Valeria Sansone, Sonia Messina, Federica Ricci, Chiara Ticci, Claudio Bruno, Caterina Agosto, Francesca Benedetti, Antonella Pini, Sabrina Siliquini, Massimiliano Filosto, Alberto Zambon, Ilaria Bitetti, Maria Rosaria Manna, Claudia Dosi, Riccardo Zanin, Stefano Parravicini, Roberto De Sanctis, Giulia Stanca, Michela Catteruccia, Michele Tosi, Irene Mizzoni, Emilio Albamonte, Valentina Franchino, Maria Sframeli, Ilaria Cavallina, Elena Procopio, Michele Sacchini, Simone Morando, Noemi Brolatti, Federica Trucco, Gaia Scarpini, Elena Briganti, Beatrice Berti, Concetta Palermo, Daniela Leone, Stefano C. Previtali, Eugenio Mercuri, the ITASMAC working group   +43 more
wiley   +1 more source

A case report of X-linked agammaglobulinemia complicated with necrotic pneumonia. [PDF]

Transl Pediatr
Zhang X, Zhu J.
europepmc   +1 more source

Intravascular papillary endothelial hyperplasia following adipose-derived mesenchymal stem cell implantation: A case report. [PDF]

JAAD Case Rep
Dhaliwal S, Rashid Z, Yang H.
europepmc   +1 more source

A Stochastic Cluster Expansion for Electronic Correlation in Large Systems. [PDF]

J Phys Chem Lett
Canestraight A, Dominic AJ, Montoya-Castillo A, Veis L, Vlcek V.   +4 more
europepmc   +1 more source

Superior Cluneal Nerve Radiofrequency Ablation for Chronic Low Back and Buttock Pain: A Technical Description and Case Series of Three Patients. [PDF]

Orthop Rev (Pavia)
Hasoon J, Viswanath O, Robinson CL, Kaye AD.   +3 more
europepmc   +1 more source

Diatomite from West Kazakhstan as a Sustainable Raw Material for Borosilicate Glass Production. [PDF]

Materials (Basel)
Satayeva S, Burakhta V, Shakeshev B, Akhmetova F, Idrisov B.   +4 more
europepmc   +1 more source