Results 11 to 20 of about 8,804 (168)
Luspatercept for Transfusion-Dependent Beta-Thalassemia: Real-World Experience in a Large Cohort of Patients From Italy. [PDF]
Am J HematolAmerican Journal of Hematology, Volume 100, Issue 9, Page 1651-1655, September 2025.Origa R, Gianesin B, Zappu A, Denotti AR, Di Giorgio MA, Sciortino R, Motta I, Panzieri DL, Rosso R, Bulla A, Culcasi M, Pasanisi AM, De Franceschi L, Di Maggio R, Pinto VM, Sanna PMG, Ricchi P, Ruffo GB, Schieppati F, Roberti D, Ferrero GB, De Michele E, Arcioni F, Fotzi I, Marktel S, Poloni A, Soverini G, Testa ER, Cabiddu G, Fortugno C, Gigante A, Polese F, Rapezzi D, Sau A, Forni GL, Cappellini MD, Longo F. +36 moreeuropepmc +2 more sourcesHydroxyurea treatment for adult sickle cell anemia patients in Kinshasa
eJHaem, Volume 4, Issue 3, Page 595-601, August 2023., 2023 Novelties:
1. This work shows the efficacy of hydroxyurea (HU) treatment of sickle cell anemia in adult patients in a low‐resource country.
2. HU treatment can result in clinical improvement despite the absence of biological changes.
3. The specific clinical relevance of this work is the need to continue treatment with HU even if clinical improvement ...Paul Lumbala Kabuyi, Gloire Mbayabo, Mamy Ngole, Aimé Lumaka Zola, Valerie Race, Gert Matthijs, Chris Van Geet, Prosper Lukusa Tshilobo, Koenraad Devriendt, Tite Minga Mikobi +9 morewiley +1 more sourceS273: LONG‐TERM ERYTHROID RESPONSE DATA FROM PATIENTS (PTS) WITH NON‐TRANSFUSION‐DEPENDENT ΒETA‐THALASSEMIA (NTDT) RECEIVING LUSPATERCEPT IN THE BEYOND TRIAL
, 2023 HemaSphere, Volume 7, Issue S3, August 2023.Ali T. Taher, Vip Viprakasit, Maria Domenica Cappellini, Antonio Giulio Piga, John B. Porter, Thomas D. Coates, Khaled M. Musallam, Gian Luca Forni, Jeevan K. Shetty, Marija Bosilkovska Weisskopf, Richard Wei, Wen‐Ling Kuo, Antonis Kattamis +12 morewiley +1 more sourceP1447: MORTALITY AND CLINICAL COMPLICATIONS AMONG PATIENTS WITH SICKLE CELL DISEASE WITH RECURRENT VASO‐OCCLUSIVE CRISES IN ITALY
, 2023 HemaSphere, Volume 7, Issue S3, August 2023.Chuka Udeze, Melanie Dovizio, Chiara Veronesi, Luca Degli Esposti, Nanxin LI, Thi Xuan Mai Patricia Dang, Gian Luca Forni +6 morewiley +1 more sourceP1449: SAFETY PROFILE OF KETOROLAC CONTINUOUS INFUSION IN SICKLE CELL RELATED ACUTE VASO‐OCCLUSIVE CRISIS
, 2023 HemaSphere, Volume 7, Issue S3, August 2023.Valeria Maria Pinto, Barbara Gianesin, Salvatore Sardo, Filippo Mazzi, Giammarco Baiardi, Sofia Menotti, Fabio Piras, Gabriele Finco, Gian Luca Forni, Lucia De Franceschi +9 morewiley +1 more sourceP1452: MORTALITY AND CLINICAL COMPLICATIONS AMONG PATIENTS WITH TRANSFUSION‐DEPENDENT BETA‐THALASSEMIA IN ITALY
, 2023 HemaSphere, Volume 7, Issue S3, August 2023.Chuka Udeze, Melanie Dovizio, Chiara Veronesi, Luca Degli Esposti, Nanxin LI, Thi Xuan Mai Patricia Dang, Gian Luca Forni +6 morewiley +1 more sourceHémoglobinurie chez l´enfant à Ouagadougou: prise en charge hospitalière et pronostic à court terme
The Pan African Medical Journal, 2019 INTRODUCTION: l’objectif de ce travail était d’analyser les aspects épidémiologiques, diagnostiques, thérapeutiques et évolutifs de l’hémoglobinurie chez l’enfant au CHU Pédiatrique Charles-De-Gaulle de Ouagadougou.Méthodes: il s’est agi d’une étude ...Hamidou Savadogo, Gérard Coulibaly, Viviane Bandaogo, Aïssata Kaboré, Lassina Dao, Sonia Kaboret, Solange Odile Ouédraogo-Yugbaré, Fla Kouéta, Diarra Yé +8 moredoaj +1 more sourceP1461: INFLAMMATORY AND SENESCENCE‐ASSOCIATED MEDIATORS AFFECT THE PERSISTENCE OF HUMORAL RESPONSE TO COVID‐19 MRNA VACCINATION IN TRANSFUSION‐DEPENDENT BETA‐THALASSEMIC PATIENTS
, 2023 HemaSphere, Volume 7, Issue S3, August 2023.Veronica Bordoni, Maddalena Casale, Valeria Maria Pinto, Rita Carsetti, Barbara Gianesin, Maria Rita Gamberini, Leila Mazdai, Susanna Barella, Anna Rita Denotti, Francesca Colavita, Silverio Perrotta, Aurelio Maggio, Lorella Pitrolo, Sabrina Quintino, Marco Caminati, Filippo Mazzi, Jacopo Ceolan, Lucia De Franceschi, Gian Luca Forni, Franco Locatelli, Chiara Agrati +20 morewiley +1 more source