Results 121 to 130 of about 937 (188)

Prenatal asfotase alfa-mediated enzyme replacement therapy restores delayed calcification in a severe infantile form of hypophosphatasia model mice [PDF]

, 2023
Hasegawa, A, Ichinohe, T, Ishizuka, S, Kasahara, M, Koshika, K, Nakamura-Takahashi, A, Umezawa, A, Yoshida, K   +7 more
core   +1 more source

Change in fracture rate and healthcare resource utilization among patients with hypophosphatasia following initiation of asfotase alfa: a retrospective US claims database analysis. [PDF]

JBMR Plus
Lyons G, Bates T, Vlasnik J, Wakeford C, Donckels EA, Chan PK, Robinson SB, Dahir KM.   +7 more
europepmc   +1 more source

Key Learnings from Clinical Research and Real-World Evidence on Asfotase Alfa Effectiveness in Hypophosphatasia: 10 Years Post-Approval. [PDF]

Adv Ther
Khan AA, Rush ET, Wakeford C, Staub D, Brandi ML.   +4 more
europepmc   +1 more source

Enzyme-replacement therapy in life-threatening hypophosphatasia [PDF]

, 2012
et al,, McAlister, William H, Whyte, Michael P   +2 more
core   +2 more sources

Odontohypophosphatasia treated with asfotase alfa enzyme replacement therapy in a toddler: a case report. [PDF]

Clin Pediatr Endocrinol, 2020
Takagi M, Kato S, Muto T, Sano Y, Akiyama T, Takagi J, Okumura A, Iwayama H.   +7 more
europepmc   +1 more source

Long-Term Outcomes of Early Enzyme Replacement Therapy With Asfotase Alfa in Perinatal Benign Hypophosphatasia: Amelioration of Bone Deformities in a Young Child. [PDF]

Cureus
Terayama S, Kobayashi M, Suemitsu T, Samura O, Oishi K.   +4 more
europepmc   +1 more source

AN ADJUNCTIVE USE OF ASFOTASE ALFA AND ZOLEDRONIC ACID AFTER SPINAL SURGERY IN NEUROFIBROMATOSIS TYPE 1 RELATED DYSTROPHIC SCOLIOSIS. [PDF]

AACE Clin Case Rep, 2020
Harindhanavudhi T, Takahashi T, Petryk A, Polly DW.   +3 more
europepmc   +1 more source

Longitudinal course of circulating miRNAs in a patient with hypophosphatasia and asfotase alfa treatment: a case report. [PDF]

JBMR Plus
Hadzimuratovic B, Haschka J, Hackl M, Diendorfer AB, Mittelbach A, Feurstein J, Zwerina J, Resch H, Kocijan R.   +8 more
europepmc   +1 more source

Effect of Asfotase Alfa on Muscle Weakness in a Japanese Adult Patient of Hypophosphatasia with Low ALP Levels. [PDF]

Intern Med, 2020
Koyama H, Yasuda S, Kakoi S, Ohata Y, Shimizu Y, Hasegawa C, Hayakawa A, Akiyama T, Yagi T, Aotani D, Imaeda K, Ozono K, Kataoka H, Tanaka T.   +13 more
europepmc   +1 more source

Hypophosphatasia: Enzyme Replacement Therapy (Asfotase Alfa) Decreases TNSALP Substrate Accumulation And Improves Functional Outcomes In Affected Adolescents And Adults [PDF]

, 2012
Greenberg, C R, Kishnani, P S, Kreher, N, Landy, H, Mack, K, Madson, K, Mhanni, A, Plotkin, H, Weber, T, Whyte, M P   +9 more
core   +1 more source