Results 171 to 177 of about 2,620 (177)
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Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
New England Journal of Medicine, 2017Richard S Finkel +2 more
exaly
Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
New England Journal of Medicine, 2017Richard Shell +2 more
exaly
Modular flexibility of dystrophin: Implications for gene therapy of Duchenne muscular dystrophy
Nature Medicine, 2002Scott Q Harper +2 more
exaly
Short Telomeres and Stem Cell Exhaustion Model Duchenne Muscular Dystrophy in mdx/mTR Mice
Cell, 2010Alessandra Sacco +2 more
exaly
ATROFIA MUSCULAR ESPINHAL TIPO I EM LACTENTE: RELATO DE CASO
2019Leonardo Magalhães Braña +5 more
openaire +1 more source
AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial
Nature Medicine, Francesco Muntoni, Craig M Mcdonald
exaly
TRATAMENTOS DISPONÍVEIS PARA ATROFIA MUSCULAR ESPINHAL: UMA REVISÃO DE LITERATURA
Laís Trovão de Carvalho +9 moreopenaire +1 more source