Results 91 to 100 of about 81,876 (149)

Assessing the efficacy of Alpha₁-Proteinase inhibitor (human) augmentation therapy for Alpha₁-Antitrypsin deficiency - Related emphysema: Challenges and opportunities. [PDF]

Heliyon
Pierce LR.
europepmc   +1 more source

Research Models and Gene Augmentation Therapy for CRB1 Retinal Dystrophies. [PDF]

Front Neurosci, 2020
Boon N, Wijnholds J, Pellissier LP.
europepmc   +1 more source

Retinal organoids with X-linked retinoschisis RS1 (E72K) mutation exhibit a photoreceptor developmental delay and are rescued by gene augmentation therapy. [PDF]

Stem Cell Res Ther
Duan C, Ding C, Sun X, Mao S, Liang Y, Liu X, Ding X, Chen J, Tang S.   +8 more
europepmc   +1 more source

Expression of Immune Checkpoints <i>LAG-3</i>, <i>CTLA-4</i>, <i>TIM-3</i>, and <i>PD-1</i> in Beta-Thalassemia Patients Treated Using HbF Augmentation Therapy and Regular Transfusions [PDF]

Turk J Haematol
Khan K, Khan U, Shah A, Shah SMI, Khan Y, Khan MTM, Rani GF.   +6 more
europepmc   +1 more source

Assessment of minimum clinically important difference in symptoms and functionality of Japanese patients with major depressive disorder following inadequate response to antidepressants: a <i>post hoc</i> analysis of the long-term study of brexpiprazole augmentation therapy in Japanese patients with major depressive disorder. [PDF]

Front Psychiatry
Hori H, Shiosakai M, Shibasaki Y, Yamato K, Zhang Y.   +4 more
europepmc   +1 more source

Alpha-1 Antitrypsin Augmentation Therapy in Chronic Pancreatitis Patients Undergoing Total Pancreatectomy and Islet Autotransplantation: A Randomized, Controlled Study. [PDF]

Cell Transplant
Wang H, Gou W, Nietert PJ, Hirsch J, Wang J, Allawi A, Mortadha AS, Cook K, Overstreet M, Wei H, Adams D, Lancaster WP, Morgan KA, Strange C.   +13 more
europepmc   +1 more source

Use of liothyronine (L-T3) as an augmentation therapy for depression during pregnancy. [PDF]

BMJ Case Rep, 2018
Bhella VS, Garg D.
europepmc   +1 more source

The Biological Effects of Double-Dose Alpha-1 Antitrypsin Augmentation Therapy. A Pilot Clinical Trial. [PDF]

Am J Respir Crit Care Med, 2019
Campos MA, Geraghty P, Holt G, Mendes E, Newby PR, Ma S, Luna-Diaz LV, Turino GM, Stockley RA.   +8 more
europepmc   +1 more source

Alpha-1 Antitrypsin Augmentation Therapy

COPD: Journal of Chronic Obstructive Pulmonary Disease, 2013
The therapy of alpha-1 antitrypsin deficiency (AATD) is an example of a medical triumph over a common hereditary disease. Based on the understanding of the pathogens of the disease as a deficiency in liver production of alpha-1 antitrypsin (AAT) resulting from inherited genetic variation in both parental AAT genes, the knowledge that A1AT functions ...
Ronald Crystal, Mark Wewers
exaly   +3 more sources