Results 231 to 240 of about 2,004,280 (291)

Health Care Transition Experiences for Rural and Urban Autistic Adolescents and Young Adults: A Qualitative Analysis. [PDF]

Autism
Zhang E, Snyder M, Alduraidi W, Hunley S, Sohl K, Cheak-Zamora N, Nelson EL.   +6 more
europepmc   +1 more source

Plasma EV Proteomics Identifies ECM Remodeling and Inflammatory Proteins LUM and C7 as Candidate Biomarkers in FSHD

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Facioscapulohumeral muscular dystrophy (FSHD) is one of the most debilitating and common muscular dystrophies. Despite its severity, no approved therapy exists for FSHD patients. However, several therapeutic candidates are currently under development, and some have recently entered clinical trials, marking the need for reliable ...
Mustafa Bilal Bayazit, Chiranth K. Nagaraj, Jackson S. Newell, Kim Truc Nguyen, Xilal Y. Rima, Jacob Doon‐Ralls, Eduardo Reátegui, Jeffrey M. Statland, Rabi Tawil, Kevin M. Flanigan, Scott Q. Harper, Nizar Y. Saad   +11 more
wiley   +1 more source

Co-Occurrence Patterns of Symptom and Functional Burden Associated with Tofacitinib and Upadacitinib: A Multidimensional Analysis of Spontaneous Reports in Rheumatoid Arthritis. [PDF]

Pharmaceutics
Yang J, Wang Y, Ma Y, Lu M, Shao F, Liu H.   +5 more
europepmc   +1 more source

Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito, Kamal Benguerba, Ken Tsuchida, Kazushige Yazawa, Isao Tsumiyama, Hiromitsu Kayama, Sandra P. Reyna, Farid Khan, Richard S. Finkel   +8 more
wiley   +1 more source

Renal Outcomes Following Autologous Stem Cell Transplantation in Dialysis-Dependent Patients With Multiple Myeloma: A Single-Center Study From a Low- and Middle-Income Country. [PDF]

Case Rep Hematol
Battat M, Khursani A, Alhendi MJ, Sawafta M, Daqa AAM, Zyoud SH, Hassan M, Asaad H, Amer R, Enaya A.   +9 more
europepmc   +1 more source

A Two‐Stage Questionnaire and Actigraphy Screening for iRBD in a Multicenter Retrospective Cohort

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective Isolated rapid‐eye‐movement sleep behavior disorder is a prodromal marker of synucleinopathies. However, most cases remain undiagnosed due to the insufficient predictive value of questionnaires and limited access to confirmatory video‐polysomnography. We assessed a two‐stage screening strategy combining a brief questionnaire on rapid‐
Caleb A. Massimi, Giorgio Ricciardiello Mejia, Andre Metzger, Kang Hyun Ryu, Salonee Marwaha, Eva Grzegorczyk, Li Zhou, Eliana Jacobs, Boris Gilyadov, Claudia Kunney, Liqhwa Ncube, Ankit Parekh, Emmanuel Mignot, Fanny M. Elahi, Joseph Winer, Kathleen Poston, Andreas Brink‐Kjaer, Emmanuel H. During   +17 more
wiley   +1 more source

Understanding Motherhood After Stroke Occurring During Pregnancy, Childbirth, or the Postpartum Period: An Exploratory Mixed-Methods Study. [PDF]

Healthcare (Basel)
Gómez-Calero C, Martín-Peralvo R, Brea-Rivero M, Pacho-Hernández JC, Fernández-Rodríguez OI.   +4 more
europepmc   +1 more source

Durable Hematologic Response in Therapy-Related Myelodysplastic Syndrome During Nivolumab Treatment for Metastatic Melanoma: A Case Report. [PDF]

Curr Oncol
Hamza FNM, Eltayeb F, Al Katari M, Ibrahim MFK.   +3 more
europepmc   +1 more source

Getting Involved Is the Key to Success. [PDF]

Dtsch Arztebl Int
Mertens S.
europepmc   +1 more source

Socioeconomic Factors and Prevalence of Functional Dependence Assessed by the Barthel Index and the Lawton-Brody Scale in the Older Population Residing in Block Hazratbal, Srinagar, India. [PDF]

Cureus
Nisar A, Malik T, Malik TZ, Khan SMS.
europepmc   +1 more source