Results 241 to 250 of about 1,231,622 (330)

CFTR modulator therapy drives microbiome restructuring through improved host physiology in cystic fibrosis: the IMMProveCF phase IV trial. [PDF]

Nat Commun
Knoll RL, Brauny MM, Robert E, Cloos L, Waser L, Hilbert K, Ulmer N, Hillen B, Birkner T, Bartolomaeus TUP, Nitsche O, Jarquín-Díaz VH, Lynch S, Gehring S, Maier L, Poplawska K, Forslund-Startceva SK.   +16 more
europepmc   +1 more source

Full Rescue of F508del-CFTR Processing and Function by CFTR Modulators Can Be Achieved by Removal of Two Regulatory Regions [PDF]

, 2020
Inna Uliyakina, Hugo M. Botelho, Ana Carina Da Paula, Sara Afonso, Miguel J. Lobo, Verónica Felício, Carlos M. Farinha, Margarida D. Amaral   +7 more
openalex   +1 more source

Effect of CFTR modulator therapy on cystic fibrosis-related diabetes.

Journal of diabetes and its complications, 2021
H. Gaines, Kellie R. Jones, Jonea Lim, Nighat F Medhi, Sixia Chen, R. Scofield   +5 more
semanticscholar   +1 more source

Antisense oligonucleotide targeting the E3 ligase RFFL potentiates CFTR modulator efficacy in CF primary bronchial epithelial cells. [PDF]

Mol Ther Nucleic Acids
Hinata D, Kai Y, Fukuda R, Kamada Y, Kasahara Y, Sasaki K, Yoshida T, Obika S, Inoue T, Okiyoneda T.   +9 more
europepmc   +1 more source

Dual CFTR modulator therapy efficacy in the real world: lessons for the future. [PDF]

ERJ Open Res, 2022
Dittrich AM, Chuang SY.
europepmc   +1 more source

WS13.2 Novel F508del-CFTR corrector that complements other CFTR modulators

Journal of Cystic Fibrosis, 2016
J.P. Miller, L. Drew, C.M. Bastos, D.J. Parks, O. Green, B. McEwan, N. Patel, S. Aghamohammadzadeh, A. Villella, K.A. Giuliano, K.A. Longo, M. Ivarsson, B. Munoz, H. Mehmet   +13 more
openaire   +1 more source

Predicting Cavg of CFTR Modulators Using Sparse Sampling: Evaluating Single and Multiple Time Points with Machine Learning Approaches [PDF]

Saly Abouelenein, A. Chalamalla, E.P. Costa, Kathleen J. Ramos, Jennifer S. Guimbellot   +4 more
openalex   +1 more source

Respiratory Muscle Function in Children and Adolescents with Cystic Fibrosis in the Era of CFTR Modulator Therapies. [PDF]

Children (Basel)
García-Pérez-de-Sevilla G, Blanco Velasco Á, Yvert T, Sanz-Santiago V, Tirado AM, López Neyra A, de Manuel C, Ruiz Valbuena M, Pérez-Ruiz M.   +8 more
europepmc   +1 more source

Real-time breath metabolomics to assess early response to CFTR modulators in adults with cystic fibrosis: an open-label proof-of-concept study [PDF]

Emmanuelle Bardin, Hélène Salvator, Camille Roquencourt, Elodie Lamy, Nicolas Hunzinger, Isabelle Sermet‐Gaudelus, Sandra de Miranda, Dominique Grenet, Philippe Devillier, Stanislas Grassin‐Delyle   +9 more
openalex   +1 more source

197: CFTR modulators and acute pancreatitis: A systematic review of the literature

, 2021
Megan Ramsey, S. Li, Stephen Kirkby, J. Heintz, Luis Lara, Darwin L. Conwell, Phil A. Hart   +6 more
openalex   +1 more source