Results 231 to 240 of about 7,856 (243)

The study of CFTR modulators in the very young

The Lancet Respiratory Medicine, 2019
openaire   +2 more sources

CFTR-​Modulation im Kindesalter

Pädiatrie & Pädologie, 2022
openaire   +1 more source

From Ivacaftor to Triple Combination: A Systematic Review of Efficacy and Safety of CFTR Modulators in People with Cystic Fibrosis

International Journal of Molecular Sciences, 2020
Andrea Gramegna, Martina Contarini, Stefano Aliberti   +2 more
exaly  

CFTR modulation for young children with cystic fibrosis

The Lancet Respiratory Medicine, 2016
Yammine, Sophie, Singer, Florian, Latzin, Philipp   +2 more
openaire   +3 more sources

Cystic fibrosis drug trial design in the era of CFTR modulators associated with substantial clinical benefit: stakeholders’ consensus view

Journal of Cystic Fibrosis, 2020
K De Boeck, Margarida D Amaral, Pavel Dřevínek   +2 more
exaly  

Neuer CFTR-Modulator

MMW - Fortschritte der Medizin
openaire   +1 more source

Discovering CFTR modulators

Nature Reviews Drug Discovery
openaire   +1 more source

Perception and participation in sport and exercise in cystic fibrosis: The impact of CFTR modulators

Respiratory Medicine
Ajay S Kasi, Lauren Lichten, William R Hunt   +2 more
exaly  

Learning from the CFTR modulator baby boom

Journal of Cystic Fibrosis
Raksha Jain, Jennifer L. Goralski
openaire   +2 more sources

Should all children with cystic fibrosis who have responsive CFTR mutations be prescribed CFTR modulators?

Journal of Cystic Fibrosis
John Massie
exaly