Results 281 to 290 of about 12,522 (293)

Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770

Proceedings of the National Academy of Sciences of the United States of America, 2009
P D J Grootenhuis
exaly  

Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial

Lancet Respiratory Medicine,the, 2015
Deborah Ashby, Katie J Bayfield, Ruaridh Buchan   +2 more
exaly  

CFTR modulation for young children with cystic fibrosis

The Lancet Respiratory Medicine, 2016
Yammine, Sophie, Singer, Florian, Latzin, Philipp   +2 more
openaire   +2 more sources

Drug Discovery Platforms for CFTR Modulators

2023
openaire   +1 more source

CFTR regulates phagosome acidification in macrophages and alters bactericidal activity

Nature Cell Biology, 2006
Chunying Li, Deborah J Nelson
exaly  

Potentiator ivacaftor abrogates pharmacological correction of ΔF508 CFTR in cystic fibrosis

Science Translational Medicine, 2014
Charles R Esther, Nikolay V Dokholyan, Scott H Randell   +2 more
exaly  

Ivacaftor treatment of cystic fibrosis in children aged 12 to <24 months and with a CFTR gating mutation (ARRIVAL): a phase 3 single-arm study

Lancet Respiratory Medicine,the, 2018
Margaret Rosenfeld, Claire E Wainwright, Steve Cunningham   +2 more
exaly  

Gating of CFTR by the STAS domain of SLC26 transporters

Nature Cell Biology, 2004
Shigeru B H Ko, Abigail Soyombo, Philip J Thomas   +2 more
exaly  

Long-Term CFTR Modulators and Changes in Hemoglobin

Annals of the American Thoracic Society, 2019
openaire   +2 more sources

462 Economic evaluation of CFTR modulators

Journal of Cystic Fibrosis
C. Lukan, C. Sakon, P. Arora
openaire   +1 more source