Results 121 to 130 of about 27,913 (221)

An Assessment of Paediatricians' Knowledge and Perspectives of Duchenne Muscular Dystrophy in Oman. [PDF]

Sultan Qaboos Univ Med J
Al Jabri Z, Alsawaie M, Saki Malehi A, Al Futaisi A, Al-Amrani F.   +4 more
europepmc   +1 more source

Vamorolone for Duchenne Muscular Dystrophy: A Cross-Trial Efficacy Comparison With Classic Corticosteroids From the FOR-DMD Trial. [PDF]

Neurology
Clemens PR, Berglund A, Schiava M, James MK, McDermott MP, Bushby K, Lampa E, Rochford ETJ, Ward LM, Griggs RC, Hoffman EP, Guglieri M.   +11 more
europepmc   +1 more source

Metabolic Complications and Ultrasound-Detected Liver Abnormalities in Paediatric Patients With Duchenne Muscular Dystrophy. [PDF]

Pediatr Obes
Śledzińska K, Polat K, Kuchta A, Dulak J, Łoboda A, Florczyk-Soluch U, Szczyrski J, Bautembach J, Meyer-Szary J, Wernio E, Lemska A, Pilarska E, Mazurkiewicz-Bełdzińska M, Irga-Jaworska N, Wierzba J.   +14 more
europepmc   +1 more source

FDA-approved antisense oligonucleotide therapies for duchenne muscular dystrophy: current status and future outlook. [PDF]

RNA Biol
Moriyama H, Moriyama S, Yokota T.
europepmc   +1 more source

Gene Editing Strategies for Duchenne Muscular Dystrophy: From Molecular Mechanisms to Clinical Translation. [PDF]

Cells
Siddika A, Rousseau J, Veillette F, Bouchard C, Lu Y, Tremblay JP.   +5 more
europepmc   +1 more source

Correction: Impact of C4BPA on Muscle progenitor cell differentiation: insights for Duchenne muscular dystrophy treatment. [PDF]

Cell Death Dis
Fernández-Simón E, Tejedera-Villafranca A, Fernández-Garabay X, Clark J, Katsikis P, Mehra P, Galloway A, Monceau A, Villalobos E, Cox D, Ramón-Azcón J, Fernández-Costa JM, Díaz-Manera J.   +12 more
europepmc   +1 more source

Genetic, Clinical, and Management Characteristics of Duchenne Muscular Dystrophy in Saudi Arabia. [PDF]

Healthcare (Basel)
AlSaman AS, Ghamdi FA, Bamaga AK, AlShaikh N, Al Muqbil M, Muthaffar O, Bashiri FA, Ali B, Qashqari H, Heider E, Itani A, Alshahrani AA, Al Muhaizea MA.   +12 more
europepmc   +1 more source

Assessing movement quality in individuals with Duchenne muscular dystrophy utilizing accelerometry: Comparisons with healthy controls. [PDF]

PLOS Digit Health
Joy N, Donnelly TJ, Soslow J, Burnette WB, Spurney C, Husain N, Gambetta K, Soriano BD, Raucci FJ, Hor K, Markham LW, Crum K, Lang CE, Miller AE, Tamaroff J, DMDCCC Investigators.   +15 more
europepmc   +1 more source

Awareness of Duchenne muscular dystrophy among medical staff in China: a multicenter cross-sectional survey. [PDF]

Front Pediatr
Zhai C, Wang J, Xia B, Guo Y, Zhang Y, Jiao Y, Shi XJ, Li H, Zhou H.   +8 more
europepmc   +1 more source

Correction: Investigating the role of EGFR signalling in muscle dystrophies: implications for Duchenne muscular dystrophy. [PDF]

Cell Death Dis
Fernández-Simón E, Tejedera-Villafranca A, Fernández-Garabay X, Clark J, Monceau A, Villalobos E, Cox D, Azcón JR, Fernández-Costa JM, Diaz-Manera J.   +9 more
europepmc   +1 more source