Results 161 to 170 of about 256,902 (295)
Ivan Shkurat, Natalya Sydorenko
openaire +1 more source
Safety and Tolerability of Givinostat: Evidence From Real‐World and Clinical Practice
ABSTRACT Objective The aim of our study was to establish the prevalence of adverse events in a real‐world setting in boys living with Duchenne muscular dystrophy (DMD) treated with givinostat as part of an Expanded Access Program (EAP) in Italy. Methods The cohort included 90 ambulant boys, with age when treatment started between 6 and 23 years (mean ...
Marika Pane +19 more
wiley +1 more source
The paradigm of NPM, like its forerunners, has been trying to answer the same question for almost twenty years: how to implement policies, strategies, programs and projects, using the market-type mechanisms, so that the institutions of the state could ...
Oehler-Sincai, Iulia Monica
core
Toward a Common Framework for Computing E-Government Index
Benchmarking and rankings, with the help of indexes and indicators, are common practices to gauge the status or standing and assess the progress of entities such as institutions & countries with respect to a characteristic or variable.
Demissie, Dawit H. +2 more
core
Unveiling the shadow economy in emerging markets. [PDF]
Duong QN, Tran NTK.
europepmc +1 more source
Early Clinical, Imaging, and Pathological Characteristics of SRPK3/TTN‐Digenic Myopathy
ABSTRACT Objective SRPK3/TTN‐digenic myopathy was recently established as a skeletal muscle myopathy caused by digenic inheritance. This study characterizes the early clinical presentation of SRPK3/TTN‐digenic myopathy in one previously reported and seven newly identified pediatric patients.
Rotem Orbach +23 more
wiley +1 more source
Dietary Diversity and Associated Factors Among Children in the Tahtay Maichew District, Northern Ethiopia. [PDF]
Reda EB +6 more
europepmc +1 more source
Compound Heterozygote Friedreich Ataxia Patients With Covert Proximal FXN Gene Deletions
ABSTRACT We present Friedreich ataxia patients with frataxin gene deletions. Data and records were collected at the Children's Hospital of Philadelphia from patients enrolled in the FACOMS natural history study. Patients with proximal deletions initially diagnosed with only one GAA expanded allele had more severe disease than their homozygous expansion
Michael P. Lazaropoulos +5 more
wiley +1 more source
Gender-related Development Index (GDI) and Gender Empowerment Measure (GEM) developed by UNDP need to be recast to realistically capture the gender gaps in development and empowerment in the Third World.
Government of India Ministry of Women and Child Development
core

