Results 101 to 110 of about 3,103 (172)
Prenatal Elexacaftor/Tezacaftor/Ivacaftor for Fetal Meconium Ileus: First Italian Case and Narrative Overview of the Emerging Evidence. [PDF]
J Clin MedBoni A, Vassallo C, Ciciriello F, Cristiani L, Mancini A, Zucaro L, Graziano S, Goffredo BM, Alghisi F, Raponi M, Fabietti I, On Behalf Of Opbg Cf Pregnancy And Fetal Therapy Multidisciplinary Group. +11 moreeuropepmc +1 more sourceVanzacaftor–tezacaftor–deutivacaftor versus elexacaftor–tezacaftor–ivacaftor in individuals with cystic fibrosis aged 12 years and older (SKYLINE Trials VX20-121-102 and VX20-121-103) : results from two randomised, active-controlled, phase 3 trials
BackgroundThe goal of cystic fibrosis transmembrane conductance regulator (CFTR) modulators is to reach normal CFTR function in people with cystic fibrosis.Fabrizzi, Benedetta, Mazurek, Henryk, Weiner, Daniel, Frederick, Carla, Calimano, Francisco, Lorenz, Michael, Sands, Dorota, Duckers, Jamie, Lam, Anna, Wilhelm, Andrew, Carroll, Mary, Fortner, Christopher, Drevinek, Pavel, Atkinson, Jeffrey, Gohy, Sophie, Jain, Raksha, Singer, Jonathan, Sermet-Gaudelus, Isabelle, Williamson, Michael, Tullis, Elizabeth, Uluer, Ahmet, Ramsey, Bonnie, Simmonds, Nicholas, Krick, Stefanie, Withers, Nicholas, Eber, Ernst, McKone, Edward, Mulrennan, Siobhain, Ahluwalia, Neil, Asensio de la Cruz, Oscar, Hoppe, Jordana, Clements, Barry, Ruddy, Jennifer, Mall, Marcus A, Owens, Louisa, Green, Deanna, Vermeulen, François, Froh, Deborah, Robinson, Philip, Waller, Michael, Staples, Heather, Moffett, Kathryn, Liou, Theodore, Mehdi, Nighat, Tremblay, Francois, Welter, John, Legg, Julian, Dacco, Valeria, O'Carroll, Mark, Linnemann, Rachel W, VX20-121-102 Study Group, [missing], Keens, Thomas, Johnson, Larry, Livingston, Floyd, Daines, Cori, Doe, Simon, Ledson, Martin, Studnicka, Michael, Elnazir, Basil, Peckham, Daniel, Bui, Stephanie, Vanderhelst, Eef, Brown, Cynthia, Olesen, Hanne, Zahigian, Rachel, Quintana-Gallego, Esther, Houdouin, Veronique, Mermis, Joel, Plant, Barry, Billings, Joanne, Trillo-Alvarez, Cesar, van der Meer, Renske, Urquhart, Don, Wang, Janice, Ren, Clement, O'Sullivan, Brian, Messore, Barbara, Haworth, Charles, Lands, Larry, Millard, Susan, Le Rouzic, Olivier, Stahl, Mirjam, Nair, Nitin, Mukadam, Zubin, Deschamps, Ashley, Horsley, Alexander, Linnane, Barry, Sutharsan, Sivagurunathan, Parkins, Michael, Appelt, Dorothea, Yonker, Lael, Altenburg, Josje, Tupayachi Ortiz, Maria Gabriela, Epaud, Ralph, Fischer Biner, Reta, Ramel, Sophie, Bakkeheim, Egil, Hilliard, Tom, Pressler, Tacjana, Brown, Sarah, Gartner, Silvia, Callison, John, Cohen-Cymberknoh, Malena, Holliday, Zachary, Marguet, Christophe, Ringshausen, Felix, Byrnes, Catherine, Cox, Desmond, Middleton, Peter, Egan, Marie, Hebestreit, Helge, Lambert, Allison, Knoop, Christiane, Cols Roig, Maria, Burr, Lucy, Mueller, Gary, Casserly, Brian, Linnemann, Rachel, Reix, Philippe, Marion, Chad, Yonker, Lael M, Goss, Christopher, Lee, Timothy, Dubin, Patricia, Wainwright, Claire, Mankikian, Julie, Schaeffer, David, Martin, Hannah, Forseen, Caralee, Blitz Castro, Enrique, Barbosa, Telma, Tolle, James, Gleiber, Wolfgang, Epton, Michael, Luna, Carmen, Salvatore, Donatello, Lindberg, Ulrika, Tirakitsoontorn, Pornchai, Sauty, Alain, Klingsberg, Ross, Michelson, Peter, Quick, Bryon, McCoy, Karen, Teneback, Charlotte, Schwarz, Carsten, McKone, Edward F, Roberts, Jon, Sosnay, Patrick R, Leroy, Sylvie, Wurth, Mark, Quon, Bradley, Manika, Katerina, Dillenhofer, Stefanie, Kremer, Ted, Lapey, Allen, Nicholson, John Michael, Kennedy, John, Henderson, Daniel, Koser, Usma, VX20-121-103 Study Group, [missing], Grenet, Dominique, Sears, Edmund, Ruiz, Fadel, Laki, Istvan, Chiron, Raphael, Efrati, Ori, van der Ent, Kors, Bilodeau, Lara, Braun, Andrew, Elidemir, Okan, Braun, Andrew T, Poplawska, Krystyna, Lopez Neyra, Alejandro, Schellhase, Dennis, Desai, Maya, Naehrig, Susanne, Homola, Lukas, Gramegna, Andrea, Ruppel, Renate, Fiel, Stanley, King, Christopher, Sapiejka, Ewa, Chmiel, James, Roukema, Jolt, Cipolli, Marco, De Monestrol, Isabelle, Omlor, Gregory, Engan, Mette, Johannes, Jimmy, Maitra, Anirban, Kotsimbos, Tom, Filbrun, Amy, DiMango, Emily, Durieu, Isabelle, Taccetti, Giovanni, Stehling, Florian, Fischer, Rainald, Lysinger, Jerimiah, Mondejar-Lopez, Pedro, Kherani, Tamizan, Pancham, Krishna, Fajac, Isabelle, Floreth, Tim, Keating, Claire, Amorim, Adelina, Kamphuis, Lieke, Scher, Herschel, Chatziagorou, Elpis, Wong, Janice, Tissot, Adrien, Wallace, James, Trimble, Aaron, Barrios, Christopher, Gilljam, Marita, Sole Jover, Amparo, Jain, Manu, Bagheri-Potthoff, Azadeh, Castellani, Carlo, Moeller, Alexander, Taylor-Cousar, Jennifer, Jia, Shijing, Escobar, Hugo, Szepfalusi, Zsolt, Sivam, Sheila, Azevedo, Pilar, Bode, Sebastian, Patel, Neil, Halasz, Adrien, Chilvers, Mark, Prais, Dario, Reyes, Santiago, Barry, Peter, Brown, Perry, Tatopoulos, Aurelie, Van Braeckel, EvaGE35UZGent0019990642098020000443910000-0002-7242-0747F85E6FEA-F0ED-11E1-A9DE-61C894A0A6B4, Taylor-Cousar, Jennifer L, Weiss, Laurence, Shkolnik, Boris, Dittrich, Anna-Maria, Morrissey, Brian, MacGregor, Gordon +240 morecore