Results 141 to 150 of about 3,864 (165)
562: Elexacaftor/tezacaftor/ivacaftor in children aged 6 and older with cystic fibrosis and at least 1 F508del allele: Interim results from a Phase 3 open-label extension study
, 2021 Félix Ratjen, Hugo Murua Escobar, Jonathan M. Gaffin, Susanna A. McColley, Erica A. Roesch, Javier Padillo–Ruiz, Claire Wainwright, Neil Ahluwalia, Christopher Chu, Sabrina Noël, Samuel M. Moskowitz, David Waltz, Tanya G. Weinstock, Jane C. Davies +13 moreopenalex +1 more source137 Long-term safety and efficacy of elexacaftor-tezacaftor-ivacaftor in children aged 2 and older with cystic fibrosis and at least one F508del allele: 48-week results of an open-label extension study
, 2023 Jennifer L. Goralski, Cori Daines, J. Pittman, Jonathan H. Rayment, P. Robinson, Rebecca Thursfield, Florian Stehling, F. Ratjen, N. Ahluwalia, Chenghao Chu, Prema R. Menon, T. Weinstock, Marcus Mall +12 moreopenalex +1 more sourcePhase 3 Open-Label Clinical Trial of Elexacaftor/Tezacaftor/Ivacaftor in Children Aged 2–5 Years with Cystic Fibrosis and at Least One F508del Allele
, 2023 Jennifer L. Goralski, Jordana E. Hoppe, Marcus Mall, Susanna A. McColley, Edward F. McKone, Bonnie Ramsey, Jonathan H. Rayment, Philip Robinson, Florian Stehling, Jennifer L. Taylor‐Cousar, Elizabeth Tullis, Neil Ahluwalia, Anna Chin, Chenghao Chu, Mengdi Lu, Tao Niu, Tanya G. Weinstock, Félix Ratjen, Margaret Rosenfeld +18 moreopenalex +1 more source173 Effectiveness of elexacaftor/tezacaftor/ivacaftor in children with cystic fibrosis: The pediatric PROMISE study
, 2022 F. Ratjen, J. Pittman, Amanda Paynter, M. Skalland, S. Heltshe, Jiaoe Xie, Leonard Couture, D. Nichols, S. Rowe, M. Rosenfeld +9 moreopenalex +1 more sourceEvaluation of Elexacafor/Tezacaftor/Ivacaftor therapy after lung transplantation in Cystic Fibrosis:The Dutch National KOALA study [PDF]
, Akkerman, Onno, Gan, C. Tji, Hansen, Carina, Heijerman, Harry G.M., Hellemons, Merel E., Luijk, Bart, Steenhuis, Willie N., van der Meer, Renske, van der Vaart, Hester, van Gemert, Anna, Verkleij, Marieke, Verschuuren, Erik, Visser, Klara A. +13 morecore +1 more source