Results 181 to 190 of about 532,411 (388)

Myocardial Storage, Inflammation, and Cardiac Phenotype in Fabry Disease After One Year of Enzyme Replacement Therapy [PDF]

, 2019
Sabrina Nordin, Rebecca Kozor, Ravi Vijapurapu, João B. Augusto, Kristopher Knott, Gabriella Captur, Thomas A. Treibel, Uma Ramaswami, Michel Tchan, Tarekegn Geberhiwot, Richard P. Steeds, Derralynn Hughes, James Moon   +12 more
openalex   +1 more source

Prenatal asfotase alfa-mediated enzyme replacement therapy restores delayed calcification in a severe infantile form of hypophosphatasia model mice

, 2023
Kaori Yoshida, Satoshi Ishizuka, Aki Nakamura-Takahashi, Akihiro Hasegawa, Akihiro Umezawa, Kyotaro Koshika, Tatsuya Ichinohe, Masataka Kasahara   +7 more
openalex   +1 more source

Functional Materials for Environmental Energy Harvesting in Smart Agriculture via Triboelectric Nanogenerators

Advanced Functional Materials, EarlyView.
This review explores functional and responsive materials for triboelectric nanogenerators (TENGs) in sustainable smart agriculture. It examines how particulate contamination and dirt affect charge transfer and efficiency. Environmental challenges and strategies to enhance durability and responsiveness are outlined, including active functional layers ...
Rafael R. A. Silva, Giulio Fatti, Emanuel Carlos, Guilherme Ferreira, Sumita Goswami, Suman Nandy, Luiz H. C. Mattoso, Elvira Fortunato, Caio G. Otoni, Rodrigo Martins   +9 more
wiley   +1 more source

Optimal therapy in Gaucher disease

Therapeutics and Clinical Risk Management, 2010
Ozlem Goker-AlpanLysosomal Diseases Research and Treatment Unit, Center for Clinical Trials, O&O Alpan LLC, Springfield, VA, USAAbstract: Gaucher disease (GD), the inherited deficiency of the lysosomal enzyme glucocerebrosidase, presents with a ...
Ozlem Goker-Alpan
doaj  

High Sustained Antibody Titers in Patients with Classic Infantile Pompe Disease Following Immunomodulation at Start of Enzyme Replacement Therapy [PDF]

, 2018
Esther Poelman, Marianne Hoogeveen‐Westerveld, Marian A. Kroos-de Haan, Johanna M. P. van den Hout, Kees J. Bronsema, Nico C. van de Merbel, Ans T. van der Ploeg, W.W.M. Pim Pijnappel   +7 more
openalex   +1 more source

A 3D Biofabricated Disease Model Mimicking the Brain Extracellular Matrix Suitable to Characterize Intrinsic Neuronal Network Alterations in the Presence of a Breast Tumor Disseminated to the Brain

Advanced Functional Materials, EarlyView.
A 3D disease model is developed using customized hyaluronic‐acid‐based hydrogels supplemented with extracellular matrix (ECM) proteins resembling brain ECM properties. Neurons, astrocytes, and tumor cells are used to mimic the native brain surrounding.
Esra Türker, Mateo S. Andrade Mier, Jessica Faber, Mike Friedrich, Zan Lamberger, Jeannette Weigelt, Christian Stigloher, Nicoletta Murenu, Natascha Schaefer, Jörg Tessmar, Gregor Lang, Silvia Budday, Katrin G. Heinze, Antje Appelt‐Menzel, Pamela L. Strissel, Reiner Strick, Carmen Villmann   +16 more
wiley   +1 more source

Time of Initiating Enzyme Replacement Therapy Affects Immune Abnormalities and Disease Severity in Patients with Gaucher Disease

, 2016
Renuka P. Limgala, Chidima Ioanou, Matthew Plassmeyer, Mark Ryherd, Lina Kozhaya, Lauren Austin, Cem Abidoglu, Derya Unutmaz, Oral Alpan, Özlem Göker-Alpan   +9 more
openalex   +2 more sources

Near‐Infrared Organic Photovoltaic Electrodes for Subretinal Neurostimulation

Advanced Functional Materials, EarlyView.
Organic photovoltaic electrodes based on the D18:Y6 blend enable precise and light‐controlled activation of retinal ganglion cells in a degenerating retina. NIR Light‐driven activation of retinal ganglion cells, tunable stimulation parameters, and biocompatibility with human retinal organoids highlight their potential for next‐generation prosthetics ...
Andrea Corna, Katarina Gugujonovic, Manuela Schiek, Alessandro Bellapianta, Paul Werginz, Amelie Ziller, Markus Clark Scharber, Ahmad Salti, Matthias Bolz, Mihai Irimia‐Vladu, Günther Zeck   +10 more
wiley   +1 more source

Profile of asfotase alfa in the treatment of hypophosphatasia: design, development, and place in therapy

Drug Design, Development and Therapy, 2018
Sasigarn A Bowden,1 Brian L Foster2 1Division of Endocrinology, Department of Pediatrics, Nationwide Children’s Hospital/The Ohio State University College of Medicine, Columbus, OH 43205, USA; 2Division of Biosciences, College of Dentistry, The ...
Bowden SA, Foster BL
doaj  

An Asymptomatic Heterozygous Female with Fabry Disease: Implications for Enzyme Replacement Therapy

, 2005
Shinichiro Inagaki, Makoto Migita, Mari Hayakawa, Atushi Fujita, Junko Yoshida, Masamichi Ishizaki, Masaharu Kotani, Hitoshi Sakuraba, Takashi Shimada, Mutsumi Murakami, Yoshitaka Fukunaga   +10 more
openalex   +2 more sources