Results 211 to 220 of about 532,411 (388)

Long‐term outcome of enzyme‐replacement therapy in advanced Fabry disease: evidence for disease progression towards serious complications [PDF]

, 2013
Frank Weidemann, Markus Niemann, Stefan Störk, Frank Breunig, Meinrad Beer, Claudia Sommer, Sandra M. Herrmann, G. Ertl, Christoph Wanner   +8 more
openalex   +1 more source

Effect of enzyme replacement therapy on the growth of patients with Morquio A

Journal of Human Genetics, 2019
C. Doherty, Molly Stapleton, Matthew Piechnik, R. Mason, W. Mackenzie, S. Yamaguchi, Hironori Kobayashi, Yasuyuki Suzuki, S. Tomatsu   +8 more
semanticscholar   +1 more source

Synthetic Nanobiology Actuated Lipometabolic Cell Factory for Autologous Tumor Immunotherapy

Advanced Functional Materials, EarlyView.
FA plays a crucial role in the interaction between tumor cells and the tumor microenvironment, especially for the immune response. A biocatalytic immunoenhancement strategy is developed to boost antitumor immunity by FA metabolic orientation to ceramide. Through the design of this delicate catalytic immunoenhancement strategy, the synthetic nanobiology
Shoujie Zhao, Yejing Zhu, Hengchao Yu, Jun Zhu, Bo Wang, Yu Qiao, Zhimin Tian, Junlong Zhao, Lei Liu   +8 more
wiley   +1 more source

Early Initiation of Enzyme Replacement Therapy in Infantile Onset Pompe Disease Improves Cardiac Outcomes: A Longitudinal Analysis. [PDF]

JIMD Rep
Cohen JL, Beaman MM, Rodriguez-Rassi E, Stafford VG, Smith PB, Landstrom AP, Kishnani PS.   +6 more
europepmc   +1 more source

The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts

Molecular Genetics and Metabolism Reports, 2019
D. Germain, P. Elliott, B. Falissard, V. Fomin, M. Hilz, A. Jovanović, I. Kantola, A. Linhart, R. Mignani, M. Namdar, A. Nowak, J. Oliveira, M. Pieroni, M. Viana-Baptista, C. Wanner, M. Spada   +15 more
semanticscholar   +1 more source

Electrochemically Driven Dissipative Growth of Affinity Hydrogels for Bioresponsive Interfaces

Advanced Functional Materials, EarlyView.
Voltage pulses drive the growth and reinforcement of hydrogel films under dissipative conditions. This biocompatible strategy enables efficient integration of affinity ligands into the hydrogel matrix, enhancing the selective capture of growth factors and allowing precise temporal control over their release, making them well‐suited as adaptive ...
Roberto Baretta, Marco Frasconi
wiley   +1 more source

Guidance for Home Enzyme Replacement Therapy in Children and Adolescents Diagnosed with Mucopolysaccharidoses: A Scoping Review Protocol. [PDF]

Int J Environ Res Public Health
Oliveira VR, Martins YNF, Araújo JIF, Silva EFD, Fuentes MB, Oliveira JSA.   +5 more
europepmc   +1 more source

RNA‐Micelles as Self‐Assembling Structures for Efficient Co‐Delivery of Synergistic siRNA and Nucleoside Analogues to Treat CRC Lung Metastasis

Advanced Functional Materials, EarlyView.
Two kinds of self‐assembled RNA micelles were used to co‐deliver synergistic siRNA and nucleoside analogues for the treatment of colorectal cancer lung metastases. Near‐complete elimination of lung cancer metastases was confirmed in an orthotopic lung metastasis model constructed using human colorectal cancer lung metastases patient surgical samples to
Kai Jin, Piotr Rychahou, Daniel W. Binzel, B. Mark Evers, Peixuan Guo   +4 more
wiley   +1 more source

Long-Term Enzyme Replacement Therapy and Renal Outcomes in Fabry Disease: A Systematic Review and Meta-Analysis. [PDF]

Biomedicines
Chen CY, Li CT, Lin CJ, Shih HM, Liu SJ, Sun FJ, Wu CJ.   +6 more
europepmc   +1 more source

Enzyme Replacement Therapy Can Reverse Pathogenic Cascade in Pompe Disease

Molecular Therapy: Methods & Clinical Development, 2020
N. Meena, E. Ralston, N. Raben, R. Puertollano   +3 more
semanticscholar   +1 more source