Results 241 to 250 of about 249,219 (350)

Amelioration of Inflammation and Metabolic Blockage in GALC Deficient Mice After Enzyme Replacement Therapy via Extracellular Vesicles. [PDF]

Int J Nanomedicine
Zelada D, Saldivia N, Samano S, George D, Chaudhari K, Nguyen D, Simchuk D, Van Breemen RB, Givogri MI.   +8 more
europepmc   +1 more source

Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII

, 2005
Carole Vogler, Beth Levy, Jeffrey H. Grubb, Nancy Galvin, Yun Tan, Emil Kakkis, Nadine Pavloff, William S. Sly   +7 more
openalex   +1 more source

Kidney Function and 24-Hour Proteinuria in Patients with Fabry Disease during 36 Months of Agalsidase Alfa Enzyme Replacement Therapy: A Brazilian Experience [PDF]

, 2009
Scheila Pretto Almeida Thofehrn, Cristina Brinckmann Oliveira Netto, Cláudia Rafaela Cecchin, Maira Graeff Burin, Úrsula da Silveira Matte, Sílvia Brustolin, Ane Cláudia Fernandes Nunes, Janice Carneiro Coelho, Marylin Tsao, Laura Bannach Jardim, Roberto Giugliani, Elvino José Guardão Barros   +11 more
openalex   +1 more source

Multifunctional Biomedical Devices with Closed‐Loop Systems for Precision Therapy

Advanced Healthcare Materials, EarlyView.
This review explores two major types of closed‐loop therapeutic systems: self‐sustained and externally triggered. It highlights recent advances in stimuli‐responsive materials, integrated bioelectronics, and data‐driven control strategies, offering insight into emerging strategies for personalized, responsive drug delivery.
Yixuan Leng, Rujie Sun
wiley   +1 more source

Pancreatic Enzyme Replacement Therapy Improves Exclusive Enteral Nutrition Related Diarrhea in Crohn's Disease: A Prospective Randomized Trial. [PDF]

United European Gastroenterol J
Mammadov S, Yağli MA, Ormeci AC.
europepmc   +2 more sources

Ambulatory electrocardiogram analysis in infants treated with recombinant human acid α-glucosidase enzyme replacement therapy for Pompe disease

, 2006
Amanda L. Cook, Priya S. Kishnani, Michael P. Carboni, Ronald J. Kanter, Y.T. Chen, Annette Ansong, Richard M. Kravitz, Henry E. Rice, Jennifer S. Li   +8 more
openalex   +1 more source

Cell Calcification Models and Their Implications for Medicine and Biomaterial Research

Advanced Healthcare Materials, EarlyView.
Calcification, is the process by which the tissues containing minerals are formed, occurring during normal physiological processes, or in pathological conditions. Here, it is aimed to give a comprehensive overview of the range of cell models available, and the approaches taken by these models, highlighting when and how methodological divergences arise,
Luke Hunter, Caterina Vanelli Coralli, Robert Dzhanaev, Aaron Morgan, Willi Jahnen‐Dechent, Sergio Bertazzo   +5 more
wiley   +1 more source

Effects of enzyme replacement therapy in sibling cases of hypophosphatasia of varying severities. [PDF]

Clin Pediatr Endocrinol
Kanno J, Nakagawa T, Miura A, Shima H, Sogi C, Kamimura M, Fujiwara I, Tachikawa K, Hino R, Michigami T, Kikuchi A.   +10 more
europepmc   +1 more source

Bone‐Derived dECM Hydrogels Support Tunable Microenvironments for In Vitro Osteogenic Differentiation

Advanced Healthcare Materials, EarlyView.
A tunable methacrylated decellularized bone matrix hydrogel (dECM‐MA) is developed to support 3D culture of human osteoblasts. The hydrogel preserves bone‐specific ECM cues and allows precise control over mechanical properties. This system provides a customizable platform for studying osteogenic differentiation and modeling bone tissue environments for
Minne Dekker, Luke Hipwood, Akhilandeshwari Ravichandran, Dietmar W. Hutmacher, Christoph Meinert, Jacqui McGovern   +5 more
wiley   +1 more source

Enzyme Replacement Therapy with Imiglucerase in a Taiwanese Child with Type 1 Gaucher Disease

, 2006
Hsiang‐Yu Lin, Shuan-Pei Lin, Chih‐Kuang Chuang, J. E. Wraith   +3 more
openalex   +1 more source