Results 91 to 100 of about 2,003 (162)

Fibrodysplasia ossificans progressiva [PDF]

, 2020
openaire   +1 more source

Single-base 2'OMe-modified LNA and MOE gapmers selectively silence <i>ACVR1</i> ^<i>R206H</i> in fibrodysplasia ossificans progressiva. [PDF]

Mol Ther Nucleic Acids
Anwar S, Hay S, Moriyama H, Mir F, Maruyama R, Yokota T.   +5 more
europepmc   +1 more source

Understanding the clinical morbidity and mortality of fibrodysplasia ossificans progressiva: a systematic literature review. [PDF]

Orphanet J Rare Dis
Harrak H, Rhee S, Souttou A, O'Meara SJ, Knox C.   +4 more
europepmc   +1 more source

An inducible knock-in mouse model of fibrodysplasia ossificans progressiva shows spontaneous formation of heterotopic ossification. [PDF]

JBMR Plus
Chakkalakal SA, Großmann NZ, Mejías Rivera L, Roberts DW, Pacifici M, Mourkioti F, Shore EM.   +6 more
europepmc   +1 more source

Assessing the economic burden and health-related quality of life in chinese patients with fibrodysplasia ossificans progressiva: a questionnaire survey analysis. [PDF]

Orphanet J Rare Dis
Xu X, He X, Wu W, Xin Y, Li Q, Song L, Li K, Wu J.   +7 more
europepmc   +1 more source

Targeting to BMP9 to restrain flare-up of fibrodysplasia ossificans progressiva. [PDF]

EMBO Mol Med
Li Q, Yuan Q.
europepmc   +1 more source

A Narrative Review of Phase II and III Clinical Trials for the Pharmacological Treatment of Fibrodysplasia Ossificans Progressiva (FOP): Efficacy, Safety, and Challenges in Treatment Strategies. [PDF]

Drug Des Devel Ther
Alharthi MS.
europepmc   +1 more source

Clinical and radiological insights into fibrodysplasia ossificans progressiva: A report on two cases. [PDF]

J Clin Orthop Trauma
Rapole S, Mehta B, Sodhai V.
europepmc   +1 more source

Fibrodysplasia Ossificans Progressiva: A Man Turned to Stone. [PDF]

Cureus
Kurtanović N, Gogić E, Džubur A, Begić E, Bijedić A.   +4 more
europepmc   +1 more source

Fibrodysplasia Ossificans Progressiva: A Case Report. [PDF]

Cureus
Qi L, Guo Y.
europepmc   +1 more source