Results 161 to 170 of about 29,070 (238)

Improvement of Bone Mineral Density in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: Results from Clinical Studies. [PDF]

J Clin Med
Zimran A, Botha J, Eastell R, Ficicioglu C, Finkelman RD, Frydman D, Giraldo P, Goker-Alpan O, Kishnani PS, Lau H, Ruhrman-Shahar N, Hughes DA.   +11 more
europepmc   +1 more source

Management of Gaucher Disease Type 1 in a Resource-Limited Setting: A Pediatric Case Study. [PDF]

Clin Case Rep
Shah BK, Koirala D, Mishra B, Sapkota R, Basnet M.   +4 more
europepmc   +1 more source

Real-World Effectiveness and Safety of Eliglustat in Adult Patients with Gaucher Disease Type 1: A Multicenter Retrospective Study in China. [PDF]

J Clin Med
Zhou Y, Hao Z, Zhuang Q, Han B.
europepmc   +1 more source

Refining Mouse Models of Gaucher Disease: Advancing Mechanistic Insights, Biomarker Discovery, and Therapeutic Strategies. [PDF]

Int J Mol Sci
Fattahi N, Ruan J, Belinsky G, Xing S, Mistry PK, Nair S.   +5 more
europepmc   +1 more source

Chronic Myeloid Leukemia Transforming into Acute Lymphoblastic Leukemia in a Patient with Gaucher Disease: A Case Report and Literature Review. [PDF]

Case Rep Oncol
Sayınalp Arslan B, Çatan Erdekli FT, Sağlam Ayhan A, Aladağ Karakulak E, Malkan ÜY, Büyükaşık Y.   +5 more
europepmc   +1 more source

MyGauch^TM: a patient-centered digital health app for Gaucher disease. [PDF]

Mhealth
Istaiti M, Shulman E, Dinur T, Frydman D, Harnevo L, Farin M, Zimran A, Revel-Vilk S.   +7 more
europepmc   +1 more source

In silico biophysics and rheology of blood and red blood cells in Gaucher Disease. [PDF]

PLoS Comput Biol
Chai Z, Li G, Ndour PA, Connes P, Buffet PA, Franco M, Karniadakis GE.   +6 more
europepmc   +1 more source

Exploring the long-term use of ambroxol in Gaucher disease type 2: insights from two pediatric cases. [PDF]

Front Neurol
Aries C, Köhn A, Täuber K, Rudolph C, Böttcher T, Bauer P, Fischer S, Muschol N.   +7 more
europepmc   +1 more source