Results 101 to 110 of about 11,644,608 (262)

Gene therapy for ALS: A review

open access: yesMolecular Therapy, 2021
Defne A. Amado, B. Davidson
semanticscholar   +1 more source

Immune Responses to Viral Gene Therapy Vectors

open access: yesMolecular Therapy, 2020
Jamie L. Shirley   +3 more
semanticscholar   +1 more source

Current Clinical Applications of In Vivo Gene Therapy with AAVs

open access: yesMolecular Therapy, 2020
J. Mendell   +12 more
semanticscholar   +1 more source

Adeno-associated virus vector as a platform for gene therapy delivery

open access: yesNature reviews. Drug discovery, 2019
Dan Wang, P. Tai, G. Gao
semanticscholar   +1 more source

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