Results 131 to 140 of about 2,049,710 (211)

Gene Therapy Techniques and Delivery Methods (Review). [PDF]

Sovrem Tekhnologii Med
Shchukina EI, Mazunin IO, Eremin II, Moskalev AA.   +3 more
europepmc   +1 more source

Rules, risks, and reality: rethinking gene therapy eligibility. [PDF]

Blood Adv
Karsenty CL, Ngwube AI.
europepmc   +1 more source

Gene Therapy Advancements in Age-Related Macular Degeneration Treatment. [PDF]

Cells
Amaxilati E, Chatzimichail E, Tsiropoulos GN, Motta L, Empeslidis T, Gatzioufas Z, Panos GD.   +6 more
europepmc   +1 more source

A novel cancer gene therapy achieving reciprocal regulation of PTEN and PARP1 expression. [PDF]

Mol Ther Oncol
Otsuka Y, Watanabe T, Kudo M.
europepmc   +1 more source

Drinkable gene therapy foam for the treatment of constrictive esophageal carcinoma. [PDF]

Gene Ther
Stephan SB, Cummings CL, Fitzgerald K, Stephan MT.   +3 more
europepmc   +1 more source

P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up*

Genetics in Medicine Open
Francesca Fumagalli, Valeria Calbi, Fabiola De Mattia, Alberto Zambon, Vera Gallo, Salvatore Recupero, Elena Sophia Fratini, Alessia Ippolito, Francesca Ciotti, Maddalena Fraschini, Marina Sarzana, Stefano Scarparo, Eugenio Montini, Sara Locatelli, Marcella Facchini, Alessandra Clerici, Francesco Morena, Sabata Martino, Muska Yarzi, Sean Moro, Andrew Shenker, Jean Brooks, Alan Richardson, Leslie Meltzer, Laura Campbell, Alessandro Aiuti   +25 more
doaj   +1 more source

Optimization of systemic AAV9 gene therapy in Niemann-Pick disease, type C1 mice. [PDF]

Life Sci Alliance
Mylvara AV, Gibson AL, Gu T, Davidson CD, Incao AA, Melnyk K, Gembic SR, Pierre-Jacques D, Cologna SM, Venditti CP, Porter FD, Pavan WJ.   +11 more
europepmc   +1 more source

Thailand's Emerging Role in the Cell and Gene Therapy Revolution: A Review of Progress and Potential. [PDF]

Clin Transl Sci
Viprakasit V, Tulalamba W, Suksangpleng T, Ekwattanakit S.   +3 more
europepmc   +1 more source