Results 141 to 150 of about 2,049,710 (211)

Chronopharmacology of AAV gene therapy in mice. [PDF]

MicroPubl Biol
Erickson P, Burr A, Parekkadan B.
europepmc   +1 more source

Balancing Promise and Peril: Hemophilia Gene Therapy Insights. [PDF]

IUBMB Life
Akula S, Borroni E, Cottonaro A, Follenzi A, Merlin S.   +4 more
europepmc   +1 more source

Precision Is Not Enough: When Tools Outpace Translation in Ocular Gene Therapy. [PDF]

Genes (Basel)
Abdalla Elsayed MEA, MacLaren RE.
europepmc   +1 more source

Qualification Criteria of Gene Therapy for Haemophilia-Opinion of the EAHAD Gene Therapy Working Group. [PDF]

Haemophilia
Miesbach W, Boban A, Chowdary P, Coppens M, Jimenez-Yuste V, Klamroth R, Mulders G, Crato M, Peyvandi F.   +8 more
europepmc   +1 more source

Advancing Gene Therapy for Pancreatitis: From Genetic Insights to Clinical Translation. [PDF]

Research (Wash D C)
Zheng YZ, Wang YC, Qi HM, Gao J, Li ZS, Liao Z, Zou WB.   +6 more
europepmc   +1 more source

AAVrh74.tMCK.NT-3 Surrogate Gene Therapy in a Mouse Model of CMT2A. [PDF]

Int J Mol Sci
Ozes B, Tong L, Moss K, Myers M, Ndengabaganizi I, Sahenk Z.   +5 more
europepmc   +1 more source

Promises past and future - Gene therapy and the actualisation of future expectations. [PDF]

Soc Sci Med
Hilberg E, Stelmach A, Kleinhout-Vliek T, Martin P.   +3 more
europepmc   +1 more source

Signals of Toxicity Associated With Gene Therapy: The Case of Etranacogene Dezaparvovec in the Treatment of Hemophilia B. [PDF]

J Pharm Technol
Castellana E, Chiappetta MR.
europepmc   +1 more source

Tks4-Targeted Gene Therapy Inhibited White Adipocyte Hypertrophy in Mice. [PDF]

FASEB J
Tian M, Deng J, Hong Y, Liu R, Li S, He X.   +5 more
europepmc   +1 more source