Results 221 to 230 of about 1,824,389 (266)

cMyBP-C in hypertrophic cardiomyopathy: gene therapy and small-molecule innovations. [PDF]

Front Cardiovasc Med
Wood PT, Seffrood MM, Colson BA, Stelzer JE.   +3 more
europepmc   +1 more source

Gene therapy in hemophilia: the dawn of a new era. [PDF]

Res Pract Thromb Haemost
Gualtierotti R, Giachi A, Bitto N, La Mura V, Peyvandi F.   +4 more
europepmc   +1 more source

Is allogeneic transplantation for sickle cell disease still relevant in the era of gene therapy? [PDF]

Blood Adv
Jones RJ, Kassim AA, Brodsky RA, DeBaun MR.   +3 more
europepmc   +1 more source

A route to engineer a genome editor for gene therapy. [PDF]

Mol Ther Nucleic Acids
Yu W, Qiao Y.
europepmc   +1 more source

Preclinical Models to Study the Molecular Pathophysiology of Meniere's Disease: A Pathway to Gene Therapy. [PDF]

J Clin Med
Nadar-Ponniah PT, Lopez-Escamez JA.
europepmc   +1 more source

The Potential of Gene Therapy in the Peritoneal Cavity

, 1999
Catherine M. Hoff, Ty R. Shockley
openalex   +1 more source

Strategies for Modifying Adenoviral Vectors for Gene Therapy. [PDF]

Int J Mol Sci
Muravyeva A, Smirnikhina S.
europepmc   +1 more source

RNA Structure: Past, Future, and Gene Therapy Applications. [PDF]

Int J Mol Sci
Haseltine WA, Hazel K, Patarca R.
europepmc   +1 more source

AAV-mediated Gene Therapy for Hereditary Deafness: Progress and Perspectives. [PDF]

Adv Sci (Weinh)
Zhang L, Tan F, Qi J, Lu Y, Wang X, Yang X, Chen X, Zhang X, Fan J, Zhou Y, Peng L, Li N, Xu L, Yang S, Chai R.   +14 more
europepmc   +1 more source