Efficacy and inhibitor development in previously treated patients with haemophilia A switched to a B domain‐deleted recombinant factor VIII [PDF]
A. Gringeri+5 more
openalex +1 more source
Alternative Immunosuppression in Acquired Haemophilia A
Haemophilia, EarlyView.
Jayna Mistry+3 more
wiley +1 more source
Estimating the Factor VIII‐Equivalent Activity of Emicizumab Using Global Assays of Haemostasis
ABSTRACT Background Emicizumab is a bispecific monoclonal antibody mimicking factor (F) VIII activity and an effective therapy for prophylaxis in people with haemophilia A (PWHA). The FVIII‐equivalent activity (FVIIIeq) of emicizumab remains unknown. Objectives To estimate FVIIIeq of emicizumab using global assays of haemostasis.
Daniel Kraemmer+6 more
wiley +1 more source
IDEAL study: A real-world assessment of pattern of use and clinical outcomes with recombinant coagulation factor IX albumin fusion protein (rIX-FP) in patients with haemophilia B in Italy. [PDF]
Tagliaferri A+27 more
europepmc +1 more source
36. Permanent Phenotypic Correction of Haemophilia B in Immunocompetent Mice by Prenatal Gene Therapy [PDF]
Andrew Gomez Vargas, Gonzalo Hortelano
openalex +1 more source
Radiological Stage of Hemophilic Arthropathy of Knee Does Not Correlate With Clinical Variables
ABSTRACT Background Various functional and radiological systems have been developed to evaluate joint health and the severity of arthropathy in hemophilic patients. Clinical relevance of these radiological systems has received minimal attention. Methods Through a retrospective chart review, 84 patients with end‐stage hemophilic arthropathy of the knee ...
Arman Vahabi+4 more
wiley +1 more source
Efficacy and safety of subcutaneous prophylaxis with dalcinonacog alfa in adults with haemophilia B. [PDF]
Mahlangu J, Levy H, Lee M, Del Greco F.
europepmc +1 more source
The molecular analysis of haemophilia B: a guideline from the UK haemophilia centre doctors’ organization haemophilia genetics laboratory network [PDF]
Mike Mitchell, S. Keeney, Anne Goodeve
openalex +1 more source
Spinal Stenosis: An Emerging Complication of Ageing in People With Haemophilia
ABSTRACT Introduction Advances in haemophilia care have brought the challenges of ageing for people with haemophilia (PWH) to the forefront. Age‐related spinal degeneration may result in spinal stenosis; however, the rates in PWH are unknown. We sought to systematically review Irish PWH to address this gap in the current literature.
Claire Kelly+19 more
wiley +1 more source
Evaluation of thrombin generating capacity in plasma from patients with haemophilia A and B [PDF]
Suzette Beguı́n+7 more
openalex +1 more source