Comparing Real-World Outcomes of Prophylaxis with Extended Half-life Factor IX (rIX-FP vs. rFIXFc and N9-GP) for Haemophilia B: An Analysis of Medical Chart Data from Germany. [PDF]
Olivieri M +8 more
europepmc +1 more source
Evaluation of coagulation disorders and iron deficiency in women with heavy menstrual bleeding
Abstract Objective To explore the incidence of congenital bleeding disorders (CBD), which may result in anemia, in a large cohort of women referred for heavy menstrual bleeding (HMB) in a specialized gynecologic unit. Methods Between January 2022 and January 2024, all women referred for HMB were screened.
Lucia Rugeri +8 more
wiley +1 more source
Real-World Unmet Needs of Patients With Haemophilia A and Haemophilia B With or Without Inhibitors: End-of-Study Results From the explorer6 Non-Interventional Study. [PDF]
Wheeler AP +14 more
europepmc +1 more source
Balancing Promise and Peril: Hemophilia Gene Therapy Insights
ABSTRACT Hemophilia is an inherited disorder characterized by impaired blood clotting caused by mutations in the genes responsible for producing coagulation factor (F) VIII (hemophilia A, HA) or FIX (hemophilia B, HB). Current treatment primarily relies on replacement therapy, involving frequent and costly infusions of FVIII or FIX concentrates.
Saicharan Akula +4 more
wiley +1 more source
Patient with a bladder cancer history presented was diagnosed with Acquired hemophilia A (AHA) according to imaging findings and laboratory tests. The parameters returned to normal after treatment of methylprednisolone and cyclophosphamide. With the recurrence of AHA, the patient was finally confirmed to have liver metastases.
Ke‐Han Zhang +4 more
wiley +1 more source
Real-world usage and effectiveness of recombinant factor IX Fc in haemophilia B from the B-SURE study in France. [PDF]
Chambost H +11 more
europepmc +1 more source
Budget impact analysis of extended half-life recombinant factor IX (rFIXFc) in the treatment of haemophilia B. [PDF]
Aiello A +4 more
europepmc +1 more source
Abstract Purpose To explore the results of a fluoroscopic‐guided intra‐osseous (IO) and intra‐articular (IA) injection of expanded adipose‐derived stromal cells (ASCs) in athletes with bone marrow lesions (BML) associated with knee osteoarthritis (OA).
Miguel A. Khoury +7 more
wiley +1 more source
Adherence and Quality of Life in Adult Patients With Haemophilia A, Haemophilia B and Von Willebrand Disease: A National Cross-Sectional Survey. [PDF]
Clausen CML +3 more
europepmc +1 more source
Haemophilia B: database of point mutations and short additions and deletions--eighth edition [PDF]
F. Giannelli
openalex +1 more source

