Indirect treatment comparison of iptacopan versus pegcetacoplan for patients with paroxysmal nocturnal hemoglobinuria and residual anemia despite C5 inhibitor treatment. [PDF]
Kulasekararaj A +9 more
europepmc +1 more source
A case of paroxysmal cold hemoglobinuria.
R, Takada +8 more
openaire +3 more sources
Epidemiology and care management of Paroxysmal Nocturnal Hemoglobinuria (PNH) in a real-world setting in France: Description from the French National Hospitalization Database. [PDF]
Peffault de Latour R +7 more
europepmc +1 more source
Paroxysmal nocturnal hemoglobinuria and eculizumab
Lucio Luzzatto +2 more
doaj +1 more source
Ravulizumab for treatment of paroxysmal nocturnal hemoglobinuria during pregnancy. [PDF]
Höchsmann B +15 more
europepmc +1 more source
Prognostic significance of PNH clones in aplastic anemia treated with immunosuppression or allogeneic HSCT: a 20-year single-center experience. [PDF]
Haroon A +11 more
europepmc +1 more source
Successful Birth After First-Trimester Ravulizumab Exposure in a Patient With Paroxysmal Nocturnal Hemoglobinuria: A Case Report. [PDF]
Morioka T +12 more
europepmc +1 more source
Paroxysmal Nocturnal Hemoglobinuria-Driven Hepatic Vein Thrombosis: A Case of Budd-Chiari Syndrome in Disguise. [PDF]
Agrawal S +4 more
europepmc +1 more source
Myeloproliferative neoplasms with clinically relevant paroxysmal nocturnal hemoglobinuria: clinical correlations and outcomes. [PDF]
Faldu P +6 more
europepmc +1 more source
Disease burden and treatment patterns of paroxysmal nocturnal hemoglobinuria in Japan: a real-world survey. [PDF]
Sakurai M +10 more
europepmc +1 more source

