Clinical Profile, Humanistic and Economic Burden of Paroxysmal Nocturnal Hemoglobinuria in Patients Treated With C5 Inhibitors. [PDF]
Gandhi S +9 more
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Paroxysmal Nocturnal Hemoglobinuria in Patients with Systemic Lupus Erythematosus: Diagnostic Challenges and Improvement with C5 Inhibitor Treatment. [PDF]
Nakata Y, Mori T, Nogami A.
europepmc +1 more source
Improved Iron Overload with Pegcetacoplan in Eculizumab-Experienced Patients with Paroxysmal Nocturnal Hemoglobinuria. [PDF]
Shammo J +4 more
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Concurrent Superior Mesenteric and Splenic Vein Thrombosis in a Prothrombin G20210A Carrier: Radiologic Evolution and Resolution on Apixaban. [PDF]
Ahmad CM +4 more
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Hepatic Sinusoidal Obstruction Syndrome Secondary to Aplastic Anemia/Paroxysmal Nocturnal Hemoglobinuria Syndrome: A Rare Case. [PDF]
Liu X, Li X, Chen Y, Huang R.
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Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry. [PDF]
Röth A +8 more
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Population PK-PD Modeling of Danicopan Add-On Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria Treated With Ravulizumab or Eculizumab. [PDF]
Chen J +4 more
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The varieties of therapeutic experience: navigating treatment options for patients with PNH. [PDF]
Bienz M, Patriquin CJ.
europepmc +1 more source
Clinical characteristics and management of paroxysmal nocturnal hemoglobinuria in the Middle East: a narrative review. [PDF]
Almakadi M +6 more
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Efficacy and safety of cyclosporine plus luspatercept versus cyclosporine in newly diagnosed non-transfusion-dependent non-severe aplastic anemia: A prospective randomized trial. [PDF]
Zhang Z +5 more
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