Results 251 to 260 of about 82,032 (316)

Rebalancing Hemostasis: Fitusiran as a First-in-Class RNAi Therapy in Hemophilia A and B. [PDF]

Health Sci Rep
Rehman RU, Fatima R, Akilimali A.
europepmc   +1 more source

QFitlia (Fitusiran): redefining hemophilia treatment with RNAi therapy. A correspondence. [PDF]

Ann Med Surg (Lond)
Lohano G, Lohano G, Lohana RR, Memon S, Lohana S, Yokolo H.   +5 more
europepmc   +1 more source

Enhancing Hemophilia A Care Through Home-Based Prophylaxis: Real-World Outcomes of a National Patient Support Program in Mexico. [PDF]

J Clin Med
Rico-Alba I, Guzmán AR, Marquez-Gonzalez H, Zurita-Cruz JN.   +3 more
europepmc   +1 more source

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial.

Blood
Matino D, Acharya SS, Taylor CT, Sun P, Agathon D, Raje S, Gould T, Palladino A, Mahlangu J, Lissitchkov T, Todorova M, Chan A, Carcao M, Sun J, Yang R, Wu R, Jin C, Zeng X, Boban A, Bilic E, Frenzel L, Fung Chan GC, Kong Li C, Apte S, Choraria N, Chistolini A, Marchesini E, Peyvandi F, Fujii T, Matsushita T, Kaneda M, Lyu CJ, Park YS, Kim S, Martinez LV, Adrian JM, Wali Y, Al Khabori M, Kurtov I, Alzahrani H, Zaher G, Micic D, Miljic P, Kostic G, Vucic M, Djurdjevic P, Hidalgo OB, Porras JG, Jiménez-Yuste V, Calvo Villas JM, Lopez Fernandez MF, Albayrak C, Okan V, Balkan C, Sahin F, Antmen A, Unal E, Visweshwar N, Sharathkumar A, Kruse-Jarres R.   +59 more
europepmc   +1 more source

Impact of prophylaxis, inhibitors, and genetics on joint outcomes according to the IPSG-MRI score in hemophilia A, B and vWD type 3. [PDF]

Front Med (Lausanne)
Seeliger A, Berg S, Glonnegger H, Boeckelmann D, Uhl M, Oldenburg J, Schlagenhauf A, Zieger B.   +7 more
europepmc   +1 more source

Emicizumab prophylaxis in a preterm infant with severe hemophilia A: a case report on the feasibility of early use. [PDF]

Res Pract Thromb Haemost
Hassan E, Percy C, Ahmed A, Lowe G, Lester W, Morgan NV, Motwani J.   +6 more
europepmc   +1 more source

Balancing Promise and Peril: Hemophilia Gene Therapy Insights. [PDF]

IUBMB Life
Akula S, Borroni E, Cottonaro A, Follenzi A, Merlin S.   +4 more
europepmc   +1 more source