Results 281 to 290 of about 82,032 (316)
Some of the next articles are maybe not open access.

Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B

New England Journal of Medicine, 2023
Steven W Pipe   +2 more
exaly  

Adeno-Associated Virus Gene Therapy for Hemophilia

Annual Review of Medicine, 2023
Lindsey A George
exaly  

Multiyear Follow-up of AAV5-hFVIII-SQ Gene Therapy for Hemophilia A

New England Journal of Medicine, 2020
K John Pasi   +2 more
exaly  

Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A

New England Journal of Medicine, 2022
Margareth C Ozelo   +2 more
exaly  

Emicizumab in Hemophilia A

New England Journal of Medicine, 2020
Tyler W, Buckner   +2 more
openaire   +3 more sources

Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A

New England Journal of Medicine, 2021
Lindsey A George   +2 more
exaly  

Hemophilia A and Hemophilia B

2019
Mariasanta Napolitano, Craig M. Kessler
openaire   +1 more source

Hemophilia A

2009
Dieter Metze   +199 more
openaire   +2 more sources

Prophylaxis versus Episodic Treatment to Prevent Joint Disease in Boys with Severe Hemophilia

New England Journal of Medicine, 2007
Marilyn J Manco-Johnson   +2 more
exaly  

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