Results 161 to 170 of about 48,006 (264)

Predicting FVIII Activity in Patients Who Use Recombinant FVIII Fc Fusion Protein for Prophylaxis and Treatment of Bleeding Episodes [PDF]

, 2014
Allen, G, Li, L, Mahlangu, JN, Pasi, J, Pierce, GF, Quon, DV, Shapiro, AD, Zhu, Y   +7 more
core  

Evaluation of kidney function and damage in patients with hemophilia B-insights from the B-Natural study. [PDF]

Res Pract Thromb Haemost
Astermark J, LeBeau P, Christensson A, Lethagen S, Berntorp E, Shapiro AD, B-Natural Study investigators.   +6 more
europepmc   +1 more source

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B. [PDF]

N Engl J Med
Reiss UM, Davidoff AM, Tuddenham EGD, Chowdary P, McIntosh J, Muczynski V, Journou M, Simini G, Ireland L, Mohamed S, Riddell A, Pie AJ, Hall A, Quaglia A, Mangles S, Mahlangu J, Haley K, Recht M, Shen YM, Halka KG, Fortner G, Morton CL, Gu Z, Hayden RT, Neufeld EJ, Okhomina VI, Kang G, Nathwani AC.   +27 more
europepmc   +1 more source

A Study of AIDS [PDF]

, 1996
Flanagan, Michael B.
core   +1 more source

Gene therapy as an innovative approach to the treatment of hemophilia B-a review. [PDF]

J Appl Genet
Wróblewska K, Bieszczad D, Popławska M, Ziętara KJ, Zajączkowska M, Filip A.   +5 more
europepmc   +1 more source

Factor IX-Padua AAV gene therapy in hemophilia B: phases 1/2 and 3 trials. [PDF]

Nat Med
Xue F, Ju M, Zhu T, Zhou Z, Sun J, Yang L, Yan Z, Zhou H, Du X, Zheng C, Zheng J, Wu X, Du Z, Jiang W, Yang C, Xiao X, Liu W, Yang R, Zhang L.   +18 more
europepmc   +1 more source

Optimization of hemophilia B treatment via population PK modeling of rIX-FP, including a 3-week regimen. [PDF]

Front Pediatr
Terasaka N, Mckeand W.
europepmc   +1 more source

Therapeutic base editing to generate a gain-of-function F9 variant for hemophilia B.

Blood
Baatartsogt N, Kashiwakura Y, Hiramoto T, Ito R, Sato R, Nagao Y, Naruoka H, Takata H, Hayakawa M, Batjargal K, Togashi T, Hoshino A, Shimizu T, Sato Y, Ishida T, Nureki O, Ohmori T.   +16 more
europepmc   +1 more source

Chinese guidance for the clinical application of adeno-associated virus vector-based gene therapy for hemophilia B (2025). [PDF]

Blood Sci
Xue F, Hu Y, Yang R, Sun J, Yang L, Wang X, Yu Z, Zhu T, Zhou H, Zhou Z, Yan Z, Du X, Zheng C, Liu W, Zhou R, Dai J, Yin J, Wang H, Tang LV, Chen S, Cheng H, Zhu M, Wang S, Song Y, Zhang P, Zhang L.   +25 more
europepmc   +1 more source

Surgery for metabolic liver disease [PDF]

, 1986
Starzl, TE
core