Results 171 to 180 of about 48,006 (264)

Hemophilia B With Intracranial Hemorrhage Rehabilitation in High-Dependency Unit: A Case Report. [PDF]

Clin Case Rep
Feng X, Zhu H, Han L, Xu H, He L.
europepmc   +1 more source

CRISPR/Cas9 mediated generation of zebrafish f9a mutant as a model for hemophilia B. [PDF]

Blood Coagul Fibrinolysis
Dhinoja S, Qaryoute AA, Deebani A, De Maria A, Jagadeeswaran P.   +4 more
europepmc   +1 more source

Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial. [PDF]

Res Pract Thromb Haemost
Klamroth R, Monahan PE, Van der Valk P, Quon D, Kazmi RS, Coppens M, O'Connell N, Pipe SW, von Drygalski A, Afzal S, Gabriel R, Youssar L, Gill S, Jansen N, Wang F, Le Quellec S, Hermans C.   +16 more
europepmc   +1 more source

Some MSM Blood Donors Move from a Lifetime Deferral to a One Year Ban “Finally” or “Not Good Enough”? [PDF]

, 2018
Printz, Heather
core   +1 more source

<i>F9</i> missense variant hot spots associated with qualitative protein defects causing hemophilia B. [PDF]

Blood Vessel Thromb Hemost
van Duijl TT, Gouw S, Kronevska I, Kooiker A, Kopatz WF, Freato N, Beijlevelt M, Hamer HM, Fijnvandraat K, Meijers JCM, van den Biggelaar M.   +10 more
europepmc   +1 more source

Extravascular factor IX after gene therapy in hemophilia B, does it matter? [PDF]

Res Pract Thromb Haemost
Van Thillo Q, Hermans C.
europepmc   +1 more source

Gene therapy for hemophilia B: results from the phase 1/2 101HEMB01/02 studies. [PDF]

Blood Adv
Pipe S, Poma A, Rajasekhar A, Everington T, Sankoh S, Allen J, Cataldo J, Crombez E.   +7 more
europepmc   +1 more source

Population Modeling of Factor IX Activity Following Administration of Fidanacogene Elaparvovec Gene Therapy in Participants with Hemophilia B. [PDF]

Clin Pharmacokinet
Wojciechowski J, Gaitonde P, Hughes JH, Ravva P.   +3 more
europepmc   +1 more source

Second gene therapy for hemophilia B approved: More answers or questions? [PDF]

Mol Ther
Kaczmarek R, Pierce GF.
europepmc   +1 more source

Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study. [PDF]

Mol Ther Methods Clin Dev
Klamroth R, Recht M, Key NS, Miesbach W, Pipe SW, Kaczmarek R, Drelich D, Salazar B, Le Quellec S, Monahan PE, Galante N, van der Valk P, Tarrant J.   +12 more
europepmc   +1 more source