Results 191 to 200 of about 12,392,515 (266)

Hemophilia B With Intracranial Hemorrhage Rehabilitation in High-Dependency Unit: A Case Report. [PDF]

Clin Case Rep
Feng X, Zhu H, Han L, Xu H, He L.
europepmc   +1 more source

Chinese guidance for the clinical application of adeno-associated virus vector-based gene therapy for hemophilia B (2025). [PDF]

Blood Sci
Xue F, Hu Y, Yang R, Sun J, Yang L, Wang X, Yu Z, Zhu T, Zhou H, Zhou Z, Yan Z, Du X, Zheng C, Liu W, Zhou R, Dai J, Yin J, Wang H, Tang LV, Chen S, Cheng H, Zhu M, Wang S, Song Y, Zhang P, Zhang L.   +25 more
europepmc   +1 more source

Optimization of hemophilia B treatment via population PK modeling of rIX-FP, including a 3-week regimen. [PDF]

Front Pediatr
Terasaka N, Mckeand W.
europepmc   +1 more source

CRISPR/Cas9 mediated generation of zebrafish f9a mutant as a model for hemophilia B. [PDF]

Blood Coagul Fibrinolysis
Dhinoja S, Qaryoute AA, Deebani A, De Maria A, Jagadeeswaran P.   +4 more
europepmc   +1 more source

China's first approved gene therapy for hemophilia B: A new era for global AAV-based treatments. [PDF]

Mol Ther
Wei H, Xiao W, Dai J.
europepmc   +1 more source

Extravascular factor IX after gene therapy in hemophilia B, does it matter? [PDF]

Res Pract Thromb Haemost
Van Thillo Q, Hermans C.
europepmc   +1 more source

<i>F9</i> missense variant hot spots associated with qualitative protein defects causing hemophilia B. [PDF]

Blood Vessel Thromb Hemost
van Duijl TT, Gouw S, Kronevska I, Kooiker A, Kopatz WF, Freato N, Beijlevelt M, Hamer HM, Fijnvandraat K, Meijers JCM, van den Biggelaar M.   +10 more
europepmc   +1 more source

Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial. [PDF]

Res Pract Thromb Haemost
Klamroth R, Monahan PE, Van der Valk P, Quon D, Kazmi RS, Coppens M, O'Connell N, Pipe SW, von Drygalski A, Afzal S, Gabriel R, Youssar L, Gill S, Jansen N, Wang F, Le Quellec S, Hermans C.   +16 more
europepmc   +1 more source

Second gene therapy for hemophilia B approved: More answers or questions? [PDF]

Mol Ther
Kaczmarek R, Pierce GF.
europepmc   +1 more source