Results 241 to 250 of about 13,086,034 (342)

Lipid Nanoparticle-Mediated Liver-Specific Gene Therapy for Hemophilia B. [PDF]

Pharmaceutics
Lohchania B, Arjunan P, Mahalingam G, Dandapani A, Taneja P, Marepally S.   +5 more
europepmc   +1 more source

118. Incorporation of a Human Replication Signal and a Superactive Factor IX Variant Stablizes and Enhances Long-Term Functional Activities Following Nonviral Gene Transfer in Hemophilia B Mice [PDF]

, 2008

openalex   +1 more source

Preclinical Evaluation of the Systemic Safety, Efficacy, and Biodistribution of a Recombinant AAV8 Vector Expressing FIX-TripleL in Hemophilia B Mice: Implications for Human Gene Therapy. [PDF]

Int J Mol Sci
Chou SC, Huang CP, Su YH, Yu CH, Yang YL, Wang SC, Lin YH, Chen YT, Li JY, Chang YT, Chen SY, Lin SW.   +11 more
europepmc   +1 more source

125. Towards a New Gene Therapy Approach for Hemophilia B Using microRNA-Regulated Lentiviral Vectors [PDF]

, 2008

openalex   +1 more source

Development of iPSC-derived FIX-secreting hepatocyte sheet as a novel treatment tool for hemophilia B treatment. [PDF]

Stem Cell Res Ther
Bayarsaikhan D, Bayarsaikhan G, Lee J, Okano T, Kim K, Lee B.   +5 more
europepmc   +1 more source

Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1

, 2004
Valder R. Arruda, Joerg Schuettrumpf, Roland W. Herzog, Timothy C. Nichols, Nancy M. Robinson, Yasmin Lotfi, Federico Mingozzi, Weidong Xiao, Linda B. Couto, Katherine A. High   +9 more
openalex   +2 more sources

643. Identification of Transgene-Specific CD4+FOXP3+ T Cells Secreting High Levels of IL-10 Following Intravascular AAV-cF.IX Gene Transfer to Muscle in Hemophilia B Dogs [PDF]

, 2009

openalex   +1 more source

Plasma levels of Human Granulocytic Elastase-alpha-Proteinase Inhibitor Complex (E-alpha1PI) in Leukemia [PDF]

, 1984
Hiller, E., Jochum, Marianne
core  

Some MSM Blood Donors Move from a Lifetime Deferral to a One Year Ban “Finally” or “Not Good Enough”? [PDF]

, 2018
Printz, Heather
core   +1 more source

Liver-directed lentiviral gene therapy in a dog model of hemophilia B

Science Translational Medicine, 2015
Alessio Cantore, M. Ranzani, C. Bartholomae, M. Volpin, P. Valle, F. Sanvito, L. Sergi, P. Gallina, F. Benedicenti, Dwight Bellinger, R. Raymer, E. Merricks, F. Bellintani, S. Martin, C. Doglioni, A. D’Angelo, T. VandenDriessche, M. Chuah, M. Schmidt, T. Nichols, E. Montini, L. Naldini   +21 more
semanticscholar   +1 more source