Results 251 to 260 of about 13,086,034 (342)

Intracranial hemorrhage in an infant leads to the diagnosis and treatment of severe hemophilia B: a case report. [PDF]

Ital J Pediatr
Lassandro G, Palladino V, Giordano P.
europepmc   +1 more source

AAV liver expression of FIX-Padua prevents and eradicates FIX inhibitor without increasing thrombogenicity in hemophilia B dogs and mice.

Blood, 2015
J. Crudele, Jonathan D. Finn, J. Siner, N. B. Martin, G. Niemeyer, Shangzhen Zhou, F. Mingozzi, C. D. Lothrop, V. Arruda   +8 more
semanticscholar   +1 more source

CRISPR/Cas9 Edition of the F9 Gene in Human Mesenchymal Stem Cells for Hemophilia B Therapy. [PDF]

Life (Basel)
Lara-Navarro IJ, Jave-Suárez LF, Marchal JA, Jaloma-Cruz AR.   +3 more
europepmc   +1 more source

603. Correction of Hemophilia B Phenotype by Novel Method of Regional Intravenous Delivery of AAV Vector to Skeletal Muscle of Hemophilia B Dogs

, 2005
Valder R. Arruda, Hansell H. Stedman, Haiyan Jian, Glenn F. Pierce, Joerg Schuettrumpf, Christian Furlan Freguia, Stefano Baila, Kapil Gopal, Timothy C. Nichols, Katherine A. High   +9 more
openalex   +1 more source

ORPHEE: A Real-World Study on rIX-FP Prophylaxis Use in Adolescent/Adult Patients With Hemophilia B. [PDF]

Eur J Haematol
Volot F, Castet S, Fournel A, Frotscher B, Gillet B, Desprez D, Tardy B, Rauch A, Chamouni P, Biron-Andreani C, Valentin JB, Harroche A, Dargaud Y, Petesch BP, d'Oiron R, Berger C, Reynes C, Lauvray T, de Raucourt E, Hassoun A, Lebreton A, Cussac V, Catovic H, Martin C, Guillet B.   +24 more
europepmc   +1 more source

[Gene therapy marks the beginning of a potential "clinical cure" for hemophilia B patients]. [PDF]

Zhonghua Xue Ye Xue Za Zhi
Zhang L.
europepmc   +1 more source

Nonacog beta pegol in previously treated children with hemophilia B: results from an international open‐label phase 3 trial

Journal of Thrombosis and Haemostasis, 2016
M. Carcao, M. Zak, F. Abdul Karim, H. Hanabusa, S. Kearney, M. Lu, P. Persson, S. Rangarajan, E. Santagostino   +8 more
semanticscholar   +1 more source

Retrospective analysis of hemophilia B in Turkey: identifying main characteristics and treatment options. [PDF]

Res Pract Thromb Haemost
Zülfikar B, Koç B, Şahin F, Şaşmaz Hİ, Kavaklı K, Balkan C, Antmen AB, Akbayram S, Güvenç B, Okan V, Türkkan E, Albayrak C, Albayrak D, Sarper N, Celkan TT, Ayyıldız O, Aksu S, Patıroğlu T, Şalcıoğlu Z, Güneş AM, Torun YA, Çalışkan Ü, Tokgöz H, Ay Y, Özdemir GN, Sönmez M, Ünal E, Öner AF, Güler N, Küpesiz OA, Ören H, Karaman S, Ünüvar A, Dağlı M, Demir AM, Söker M, Alioğlu B, Kaya Z, Ayhan AC, Bıçakçı Z, Aral YZ, Ar MC.   +41 more
europepmc   +1 more source

Hemophilia B in a Crossbred Maltese Dog

, 2006
Makoto Nakata, Manabu Sakai, Takeo Sakai
openalex   +2 more sources

Management of US men, women, and children with hemophilia and methods and demographics of the Bridging Hemophilia B Experiences, Results and Opportunities into Solutions (B‐HERO‐S) study

European Journal of Haematology, 2017
T. Buckner, M. Witkop, C. Guelcher, M. Frey, S. Hunter, S. Peltier, M. Recht, C. Walsh, C. Kessler, Wendy E. Owens, David B Clark, N. Frick, Michelle Rice, N. Iyer, N. Holot, D. Cooper, R. Sidonio   +16 more
semanticscholar   +1 more source