Results 151 to 160 of about 1,275 (171)
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Idursulfase

Reactions Weekly, 2023
openaire   +1 more source

Idursulfase

Reactions Weekly, 2018
openaire   +2 more sources

Comparison of cognitive function in siblings with neuronopathic mucopolysaccharidosis type II: Evaluation of early treatment with intravenous idursulfase and intrathecal idursulfase-IT

Molecular Genetics and Metabolism, 2021
Joseph Muenzer   +11 more
openaire   +1 more source

Idursulfase

Reactions Weekly, 2010
openaire   +2 more sources

Idursulfase/prednisolone

Reactions Weekly, 2021
openaire   +1 more source

Idursulfase

Reactions Weekly, 2011
openaire   +1 more source

Idursulfase

Reactions Weekly, 2016
openaire   +1 more source

[Clinical study of enzyme replacement therapy with idursulfase].

Revista de neurologia, 2008
Important advances have been made in enzyme replacement therapy in the treatment of lysosomal diseases over the last two decades. Here we review the initial ERT trial using idursulfase in Hunter syndrome (mucopolysaccharidosis type II) and we also examine relevant aspects of the use of this enzyme.A preclinical trial in a knockout mouse showed a ...
openaire   +1 more source

Idursulfase

Reactions Weekly, 2012
openaire   +1 more source

Immune modulation in a patient with mucopolysaccharidosis II (MPSII) on idursulfase therapy with high titer anti-idursulfase antibodies

Molecular Genetics and Metabolism, 2013
Barbara Burton   +4 more
openaire   +1 more source

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