Results 61 to 70 of about 670,775 (252)
Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito +8 more
wiley +1 more source
Background: The Pacific Least Developed Countries (LDCs)—Kiribati, the Solomon Islands, Tuvalu, and Vanuatu—are among the countries most vulnerable to climate variability and change.
Kristie Ebi, ProfPhD, Chris Boyer, MPH
doaj +1 more source
ABSTRACT Objective Building on our prior Behavioral Risk Factor Surveillance System analysis identifying adults aged 18–39 as the primary driver of the national increase in self‐reported cognitive disability, we examined factors associated with this rise using 2013–2024 U.S. BRFSS data. Methods We analyzed U.S.
Adam de Havenon +9 more
wiley +1 more source
Cognitive Behavioral Therapy for Youth With Childhood‐Onset Lupus: A Randomized Clinical Trial
Objective Our objective was to determine the feasibility and acceptability of the Treatment and Education Approach for Childhood‐Onset Lupus (TEACH), a six‐session cognitive behavioral intervention addressing depressive, fatigue, and pain symptoms, delivered remotely to individual youth with lupus by a trained interventionist.
Natoshia R. Cunningham +29 more
wiley +1 more source
Is the process of graduation of least developed countries (LDCS) suitable and sufficient?
Millions of people are living in the Least Developed Countries (LDCs), the poorest of the poor. Getting them out of that situation is one of humanity’s most urgent tasks.
Margarita Navarro-Pabsdorf +3 more
doaj +1 more source
The COVID-19 pandemic, the Sustainable Development Goals on health and education and "least developed countries" such as Nepal. [PDF]
Regmi KD.
europepmc +1 more source
Objective Mycophenolate mofetil (MMF) use in limited cutaneous systemic sclerosis (lcSSc) is relatively uncommon because of the lower fibrotic burden and the predominance of vascular complications. In vitro observations and clinical data from transplanted patients suggest a protective effect of MMF on endothelial function.
Enrico De Lorenzis +77 more
wiley +1 more source
The Pacific Small Island Developing State (SIDS) of Kiribati has met the formal, minimal criteria for graduation from the Least Developed Country (LDC) category of the United Nations on multiple occasions from 2003 to 2018. Nevertheless, in light of both
Edoardo Monaco, Masato Abe
doaj +1 more source
Objective Systemic lupus erythematosus (SLE) is a heterogenous inflammatory condition with widely varying global prevalence estimates. The frequency of SLE in the general population of Australia has been reported to be notably lower than contemporary estimates in countries such as the United States or United Kingdom, at 19 to 39 per 100,000 as opposed ...
Lucinda Roper +7 more
wiley +1 more source

