Results 151 to 160 of about 7,348 (160)

Novel candidate disease for gene therapy: metachromatic leukodystrophy

Expert Opinion on Biological Therapy, 2007
Alessandra Biffi, Luigi Naldini
exaly  

Clinicopathological differences between juvenile and late infantile metachromatic leukodystrophy

Brain and Development, 1981
Haruomi Nakamura
exaly  

A Semi-Automatic Algorithm for Determining the Demyelination Load in Metachromatic Leukodystrophy

Academic Radiology, 2012
Marko Wilke, Samuel Groeschel
exaly  

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial

Lancet, The, 2016
Mariaclelia Stefania di Serio, Francesca Fumagalli, Paola M V Rancoita   +2 more
exaly  

Metachromatic Leukodystrophy and Its Effects on the Gallbladder: A Case Report

Ultrastructural Pathology, 2011
exaly  

Pathology of the Gallbladder in a Child with Metachromatic Leukodystrophy

Pediatric and Developmental Pathology, 2015
Sarangarajan Ranganathan
exaly  

Low arylsulphatase A activity in a family without metachromatic leukodystrophy

Clinical Genetics, 1978
exaly  

Gene therapy of metachromatic leukodystrophy

Expert Opinion on Biological Therapy, 2005
exaly  

Metachromatic Leukodystrophy and Coincidental Finding of Papillomatosis of the Gallbladder. A Case Report

Neuropediatrics, 1995
exaly  

Metachromatic leukodystrophy: genetics, pathogenesis and therapeutic options

Acta Paediatrica, International Journal of Paediatrics, 2008
exaly