Results 121 to 130 of about 1,106 (130)

Assessment of plasma lyso-Gb3 for clinical monitoring of treatment response in migalastat-treated patients with Fabry disease

Genetics in Medicine, 2021
Atul Mehta, Christiane Auray-Blais, Raphael Schiffmann   +2 more
exaly  

Treatment of Fabry Disease management with migalastat—outcome from a prospective 24 months observational multicenter study (FAMOUS)

European Heart Journal - Cardiovascular Pharmacotherapy, 2022
Anibh M Das, Nurcan Üçeyler, Malte Lenders   +2 more
exaly  

Pharmacometric model of agalsidase–migalastat interaction in human: a novel mechanistic model of drug-drug interaction between a therapeutic protein and a small molecule

Journal of Pharmacokinetics and Pharmacodynamics, 2022
Thanh Bach, Guohua An
exaly  

Efficacy and safety of migalastat in a Japanese population: a subgroup analysis of the ATTRACT study

Clinical and Experimental Nephrology, 2019
Ichiei Narita, Jay Barth, Toya Ohashi
exaly  

Fabry disease genotype, phenotype, and migalastat amenability: Insights from a national cohort

Journal of Inherited Metabolic Disease, 2020
Felix Beuschlein, Frédéric Barbey, Albina Nowak   +2 more
exaly  

Inter-assay variability influences migalastat amenability assessments among Fabry disease variants

Molecular Genetics and Metabolism, 2019
Muthuraman Meiyappan, Andrey Gurevich
exaly  

Pharmacokinetics, safety, and tolerability following single-dose migalastat hydrochloride (GR181413A/AT1001) in healthy male Japanese subjects

Journal of Drug Assessment, 2013
Takumi Terao
exaly  

Relative bioavailability and the effect of meal type and timing on the pharmacokinetics of migalastat in healthy volunteers

Clinical Pharmacology in Drug Development, 2015
exaly  

A Systematic Review on Safety and Efficacy of Migalastat for the treatment of Fabry’s Disease

Expert Opinion on Pharmacotherapy
Nidhi B. Agarwal
exaly  

Pathogenicity of novel ene missense mutations in Fabry disease and the therapeutic impact of migalastat

Journal of Advanced Research
Pengcheng Ji
exaly