Results 151 to 160 of about 21,613 (172)

Understanding the Early Presentation of Mucopolysaccharidoses Disorders: Results of a Systematic Literature Review and Physician Survey

FIRE Forum for International Research in Education, 2018
Hatice Serap Sivri, Roberto Giugliani, Klane K White   +2 more
exaly  

Prevalence rates of mucopolysaccharidoses in Poland

Journal of Applied Genetics, 2014
Anna Tylki-Szymanska, Agnieszka Ługowska, Agnieszka Jurecka   +2 more
exaly  

Gene therapy for mucopolysaccharidosis

Expert Opinion on Biological Therapy, 2007
Katherine P Ponder, Mark E Haskins
exaly  

Incidence of the mucopolysaccharidoses in Western Australia

American Journal of Medical Genetics, Part A, 2003
John Nelson
exaly  

Incidence of the mucopolysaccharidoses in Taiwan, 1984–2004†

American Journal of Medical Genetics, Part A, 2009
Wuh-liang Hwu, Chih-Kuang Chuang, HY Lin
exaly  

A Blood-Brain-Barrier-Penetrating Anti-human Transferrin Receptor Antibody Fusion Protein for Neuronopathic Mucopolysaccharidosis II

Molecular Therapy, 2018
Kohtaro Minami, Yuri Koshimura, Hideto Morimoto   +2 more
exaly  

Anaesthesia for Children with Mucopolysaccharidoses

Anaesthesia and Intensive Care, 1996
T C K Brown, T C Brown, C Moores
exaly  

Emerging drugs for the treatment of mucopolysaccharidoses

Expert Opinion on Emerging Drugs, 2016
Filippo Vairo, Luciana Giugliani, Roberto Giugliani   +2 more
exaly