Results 151 to 160 of about 5,240 (183)

Biomarkers in patients with mucopolysaccharidosis types II and IV

Molecular Genetics and Metabolism, 2019
Shunji Tomatsu, Honoka Fujitsuka, Kazuki Sawamoto   +2 more
openaire   +1 more source

A Blood-Brain-Barrier-Penetrating Anti-human Transferrin Receptor Antibody Fusion Protein for Neuronopathic Mucopolysaccharidosis II

Molecular Therapy, 2018
Hideto Morimoto, Yuri Koshimura, Ryuji Yamamoto   +2 more
exaly  

Anesthesia for an adult with mucopolysaccharidosis I

Journal of Clinical Anesthesia, 2005
John L Ard, Alex Bekker, Anthony K Frempong-Boadu   +2 more
exaly  

Outcomes of Long-Term Treatment with Laronidase in Patients with Mucopolysaccharidosis Type I

Journal of Pediatrics, 2016
Jean Mercer, Jane Ashworth
exaly  

Early Clinical Markers of Central Nervous System Involvement in Mucopolysaccharidosis Type II

Journal of Pediatrics, 2011
Joshua B Holt, Michele D Poe, Maria L Escolar   +2 more
exaly  

Mucopolysaccharidosis Type II: One Hundred Years of Research, Diagnosis, and Treatment

International Journal of Molecular Sciences, 2020
Francesca D’Avanzo, Laura Rigon, Alessandra Zanetti   +2 more
exaly  

Population-Based Newborn Screening for Mucopolysaccharidosis Type II in Illinois: The First Year Experience

Journal of Pediatrics, 2019
George E Hoganson, Dorothy K Grange
exaly  

Update of treatment for mucopolysaccharidosis type III (sanfilippo syndrome)

European Journal of Pharmacology, 2020
Yan Meng
exaly  

Gene therapy for mucopolysaccharidosis

Expert Opinion on Biological Therapy, 2007
Katherine P Ponder
exaly  

Airway-Related Symptoms and Surgeries in Patients With Mucopolysaccharidosis I

Annals of Otology, Rhinology and Laryngology, 2015
Iain A Bruce, James E Wraith
exaly