Results 321 to 330 of about 433,578 (358)

Therapeutic approaches for Duchenne muscular dystrophy

Nature Reviews Drug Discovery, 2023
Thomas C Roberts, Kay E Davies
exaly  

Muscular diseases

2014
Roger Langford, David Ashton-Cleary
openaire   +1 more source

Spinal muscular atrophy

Nature Reviews Disease Primers, 2022
Francesco Muntoni, Richard S Finkel
exaly  

Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy

Nature Medicine, 2020
Alessandra Moretti, Daniel Sinnecker, Shicheng Sun   +2 more
exaly  

Spinal bulbar muscular atrophy—Kennedy's disease

QJM: An International Journal of Medicine, 2023
Xiao, Deng, Eng-King, Tan
openaire   +2 more sources

[MUSCULAR DISEASES].

Harefuah, 1996
S A, WEISMAN, M, COHN
openaire   +1 more source

Induced pluripotent stem cells from a spinal muscular atrophy patient

Nature, 2008
Allison D Ebert, Christian L Lorson, Clive N Svendsen   +2 more
exaly  

Metabolic disease: Muscular fat burning

Lipidomics Gateway, 2010
openaire   +2 more sources

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

Nature Medicine, 2019
Christopher E Nelson, Yaoying Wu, Matthew A Waller   +2 more
exaly  

Defective membrane repair in dysferlin-deficient muscular dystrophy

Nature, 2003
Steven S Vogel, Chien-Chang Chen, Kevin P Campbell   +2 more
exaly