Results 151 to 160 of about 71,356 (167)

Caregivers and multidisciplinary team members' perspectives on shared decision making in Duchenne muscular dystrophy: A qualitative study. [PDF]

Orphanet J Rare Dis
Schoefs E, Desmet T, Lerinckx E, Waele L, Geuens S, Pelicaen C, Meeus L, Simoens S, Audenhove CV, Mommen M, Janssens R, Huys I.   +11 more
europepmc   +1 more source

Expansion of Splice-Switching Therapy with Antisense Oligonucleotides. [PDF]

Int J Mol Sci
Takeshima Y.
europepmc   +1 more source

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Neurodevelopmental, behavioral, and emotional symptoms common in Duchenne muscular dystrophy

Muscle and Nerve, 2020
We studied neurodevelopmental and behavioral/emotional symptoms in patients with Duchenne muscular dystrophy (DMD).
A. Darmahkasih, I. Rybalsky, C. Tian, K. Shellenbarger, P. Horn, J. Lambert, B. Wong   +6 more
semanticscholar   +1 more source

Golodirsen for Duchenne muscular dystrophy.

Drugs of Today, 2020
Duchenne muscular dystrophy (DMD) is a life-shortening X-linked genetic disorder characterized by progressive wasting and weakening of muscles in boys. Loss-of-function mutations in the DMD gene, which codes for dystrophin, lead to this disease.
S. Anwar, T. Yokota
semanticscholar   +1 more source

The Genetic Relationship of Progressive Muscular Dystrophy (Duchenne Type) and Mental Retardation

Developmental Medicine & Child Neurology, 1968
H. Cohen, G. Molnar, L. T. Taft
semanticscholar   +1 more source

Dystrophin: The protein product of the duchenne muscular dystrophy locus

Cell, 1987
Eric P. Hoffman, Robert H. Brown, Louis M. Kunkel   +2 more
semanticscholar   +1 more source

[Muscular dystrophy: Duchenne and Becker-Kiener types].

Deutsche Medizinische Wochenschrift, 1979
E. Kuhn
semanticscholar   +1 more source