Results 141 to 150 of about 6,546 (245)

Stabilization of Respiratory Function in Pediatric Spinal Muscular Atrophy Treated with Nusinersen [PDF]

, 2020
Archana Chacko, S. Deegan, Peter D. Sly, Leanne Gauld   +3 more
openalex   +1 more source

Mid- and long-term (at least 12 months) follow-up of patients with spinal muscular atrophy (SMA) treated with nusinersen, onasemnogene abeparvovec, risdiplam or combination therapies: A systematic review of real-world study data [PDF]

, 2022
Judit Erdös, Claudia Wild
openalex   +1 more source

Cerebrospinal fluid characteristics of patients treated with intrathecal nusinersen for spinal muscular atrophy [PDF]

, 2022
Rotem Orbach, Liora Sagi, Efraim Sadot, Itay Tokatly Latzer, Anna Shtamler, Tehila Zisberg, Aviva Fattal‐Valevski   +6 more
openalex   +1 more source

POSB339 Real-World Adherence of Nusinersen for the Treatment of Spinal Muscular Atrophy (SMA) Using US Large Administrative Claims Dataset [PDF]

, 2022
Nicole B. Johnson, Qiang Hou, AD Paradis, Crystal M. Proud, Bora Youn   +4 more
openalex   +1 more source

CRISPRi-based radiation modifier screen identifies long non-coding RNA therapeutic targets in glioma. [PDF]

, 2020
BackgroundLong non-coding RNAs (lncRNAs) exhibit highly cell type-specific expression and function, making this class of transcript attractive for targeted cancer therapy.
Akeson, Mark, Birk, Harjus S, Gupta, Nalin, He, Daniel, Hong, Sung Jun, Horlbeck, Max A, Jain, Miten, Koontz, Mark, Lien, Brian V, Lim, Daniel A, Liu, S John, Malatesta, Martina, Monje, Michelle, Olsen, Hugh E, Pedraza, Leslie, Raleigh, David R, Saha, Parna, Seo, Kyounghee, Thombare, Shivani S, Ullian, Erik M, Weissman, Jonathan S   +20 more
core   +1 more source

P.166 Subcutaneous intrathecal catheter and port implants for administration of Nusinersen in patients with Spinal Muscular Atrophy [PDF]

, 2022
A Bokeris, D Mcneely, J Sheriko
openalex   +1 more source

An observational cohort study on pulmonary function in adult patients with 5q-spinal muscular atrophy under nusinersen therapy [PDF]

, 2023
Bogdan Bjelica, Camilla Wohnrade, Alma Osmanovic, Olivia Schreiber‐Katz, Susanne Petri   +4 more
openalex   +1 more source

Computed tomography-guided transforaminal lumbar puncture using local anesthesia and a straight 22-gauge spinal needle for intrathecal nusinersen in adults: Findings in 77 procedures

, 2021
Mougnyan Cox, Kofi‐Buaku Atsina, Preethi Ramchand, Jonathan Ji, Neda I. Sedora-Román, Bryan Pukenas   +5 more
openalex   +2 more sources

Improvement of muscle strength in specific muscular regions in nusinersen-treated adult patients with 5q-spinal muscular atrophy [PDF]

, 2023
Olivia Schreiber‐Katz, Hannah Siegler, Gary Wieselmann, Mareike Kumpe, Gresa Ranxha, Susanne Petri, Alma Osmanovic   +6 more
openalex   +1 more source

Early experiences of nusinersen for the treatment of spinal muscular atrophy: Results from a large survey of patients and caregivers

, 2020
Er Chen, Stacy Dixon, Rupali Naik, Josh Noone, J.D. Buchenberger, Sarah Whitmire, Rosalina Mills, W. David Arnold   +7 more
openalex   +1 more source