Results 141 to 150 of about 6,101 (249)

POSB339 Real-World Adherence of Nusinersen for the Treatment of Spinal Muscular Atrophy (SMA) Using US Large Administrative Claims Dataset [PDF]

, 2022
Nicole B. Johnson, Qiang Hou, AD Paradis, Crystal M. Proud, Bora Youn   +4 more
openalex   +1 more source

P.166 Subcutaneous intrathecal catheter and port implants for administration of Nusinersen in patients with Spinal Muscular Atrophy [PDF]

, 2022
A Bokeris, D Mcneely, J Sheriko
openalex   +1 more source

An observational cohort study on pulmonary function in adult patients with 5q-spinal muscular atrophy under nusinersen therapy [PDF]

, 2023
Bogdan Bjelica, Camilla Wohnrade, Alma Osmanovic, Olivia Schreiber‐Katz, Susanne Petri   +4 more
openalex   +1 more source

Why antisense could make sense for neurodegeneration [PDF]

, 2017
Massey, Thomas, Robertson, Neil
core   +1 more source

Respiratory outcomes post nusinersen in spinal muscular atrophy type 1

, 2020
Kate Gonski, Dominic A. Fitzgerald
openalex   +1 more source

Improvement of muscle strength in specific muscular regions in nusinersen-treated adult patients with 5q-spinal muscular atrophy [PDF]

, 2023
Olivia Schreiber‐Katz, Hannah Siegler, Gary Wieselmann, Mareike Kumpe, Gresa Ranxha, Susanne Petri, Alma Osmanovic   +6 more
openalex   +1 more source

Intrathecal administration of Nusinersen in children and adolescent SMA type 1 and 2 [PDF]

, 2023
Michele Michelin Becker, Lygia Ohlweiler, Josiane Ranzan, Hugo Leonardo Justo Horácio, Ana Clara Bernardi Saul, Layanna Bezerra Maciel Pereira, Renata Yasmin Cardoso Sousa, Dayana de Lima Mariano, Rudimar dos Santos Riesgo   +8 more
openalex   +1 more source

Clinical Outcome of Adult Spinal Muscular Atrophy Patients Treated with Nusinersen: A Case Series Review

, 2020
Keng Lam, Abel Wu
openalex   +2 more sources

Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study

, 2019
Darryl C. De Vivo, Enrico Bertini, Kathryn J. Swoboda, Wuh‐Liang Hwu, Thomas O. Crawford, Richard S. Finkel, Janbernd Kirschner, Nancy L. Kuntz, Julie Parsons, Monique M. Ryan, Russell J. Butterfield, Haluk Topaloğlu, Tawfeg Ben‐Omran, Valeria Sansone, Yuh‐Jyh Jong, Francy Shu, John F. Staropoli, Douglas A. Kerr, Alfred Sandrock, Christopher Stebbins, Marco Petrillo, Gabriel Braley, Kristina Johnson, Richard Foster, Sarah Gheuens, Ishir Bhan, Sandra P. Reyna, Stephanie Fradette, Wildon Farwell   +28 more
openalex   +1 more source

Early experiences of nusinersen for the treatment of spinal muscular atrophy: Results from a large survey of patients and caregivers

, 2020
Er Chen, Stacy Dixon, Rupali Naik, Josh Noone, J.D. Buchenberger, Sarah Whitmire, Rosalina Mills, W. David Arnold   +7 more
openalex   +1 more source