Results 231 to 240 of about 6,546 (245)
Some of the next articles are maybe not open access.
Plecanatide, Nusinersen, and Obeticholic acid
Journal of the American Pharmacists Association, 2017Daniel A. Hussar, Deborah K. Douglas
openaire +3 more sources
Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy
Nature Neuroscience, 2017Nusinersen (Spinraza) is a recently approved drug for treating spinal muscular atrophy. Approval of nusinersen may signal new opportunities for using antisense oligonucleotides as treatments for devastating neurological diseases.
openaire +2 more sources
A CSF marker of nusinersen treatment response
Nature Reviews Neurology, 2022openaire +2 more sources
Intrathecal nusinersen administration: Is anesthesia really needed?
Pediatric Anesthesia, 2021Anna Camporesi +2 more
openaire +3 more sources
Transforaminal lumbar puncture for intrathecal nusinersen administration
Muscle & Nerve, 2018Adam Evans +4 more
openaire +2 more sources
Nusinersen in adults with spinal muscular atrophy: new challenges
The Lancet Neurology, 2020Valeria A. Sansone +2 more
openaire +3 more sources

