Results 241 to 249 of about 6,101 (249)
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Nusinersen treatment of spinal muscular atrophy: current knowledge and existing gaps
Developmental Medicine and Child Neurology, 2019Laurent Servais, Laurent Servais
exaly
Nusinersen im Kindesalter und bei Erwachsenen [PDF]
openaire +1 more source
Cost-effectiveness of Nusinersen for Spinal Muscular Atrophy
JAMA Pediatrics, 2018openaire +3 more sources
Nusinersen: A Treatment for Spinal Muscular Atrophy
Annals of Pharmacotherapy, 2019Debra L Stevens, Cheri Walker
exaly
Nusinersen improves walking distance and reduces fatigue in later‐onset spinal muscular atrophy
Muscle and Nerve, 2019Basil T Darras+2 more
exaly
Nusinersen Found Promising for Spinal Muscular Atrophy
Neurology Today, 2017openaire +2 more sources
Cost-effectiveness of Nusinersen for Spinal Muscular Atrophy—Reply
JAMA Pediatrics, 2018openaire +3 more sources
Funktionelle Verbesserungen mit Nusinersen in allen Altersgruppen
DNP – Die Neurologie & Psychiatrieopenaire +1 more source