Results 91 to 98 of about 285 (98)

Successful omalizumab use after failed desensitization in olipudase alfa-induced anaphylaxis

Molecular Genetics and Metabolism
Carolina S. Aranda, Sandra Kyosen, Ana Maria Martins   +2 more
openaire   +1 more source

Elastoresonance as a surveillance tool in a patient with acid sphingomyelinase deficiency undergoing treatment with olipudase alfa

Molecular Genetics and Metabolism
Magdalena Ceron-Rodriguez, Carlos P. Acosta Rodríguez Bueno, Judith Almanza-Aranda, Alan E. Araujo Carrillo, Karla Cifuentes-Uribe   +4 more
openaire   +1 more source

Case report: Treatment of the severe ASMD phenotype with olipudase alfa and JZP-150

Molecular Genetics and Metabolism
Justin Hopkin, Steven Laffoon, Joy Chen, Sophia Abner   +3 more
openaire   +1 more source

Efficacy and Safety of Olipudase Alfa for the Treatment of Acid Sphingomyelinase Deficiency ( ASMD ): A Systematic Review and Meta‐Analysis

American Journal of Medical Genetics, Part A
Paulo V Z Ribeiro, Giovanna Giovacchini Dos Santos, Albuquerque Alb   +2 more
exaly  

Olipudase alfa in adult and pediatric ASMD patients: Interim results from French early access program

Molecular Genetics and Metabolism
Nathalie Guffon, Nadia Belmatoug, Nihal Martis, Christian Lavigne, Karin Mazodier, Achille Aouba, Anne Christophe, Olivier Lidove   +7 more
openaire   +1 more source

Novel Case of Olipudase Alfa Enzyme Replacement Therapy to Treat Niemann-Pick Disease Type-B Following Lung Transplant

The Journal of Heart and Lung Transplantation
J. Ng, G.F. Watts, M. Musk, J. Wrobel, M. Lavender, S. Lawrence, C.J. Welman, C. Wood, J. Polce, M. Yaw   +9 more
openaire   +1 more source

Review for "Olipudase alfa-related anaphylaxis prevented by omalizumab and tailored desensitization protocol in acid sphingomyelinase deficiency"

openaire   +2 more sources

Decision letter for "Olipudase alfa-related anaphylaxis prevented by omalizumab and tailored desensitization protocol in acid sphingomyelinase deficiency"

openaire   +1 more source