Results 101 to 110 of about 166,938 (112)

Efficacy and safety of olipudase alfa in children: A real-life case report

Molecular Genetics and Metabolism
Lucas Ferreira Teixeira, Alícia D. Dornelles, Fabiano Poswar, Ida Vanessa D. Schwartz   +3 more
openaire   +1 more source

Sustained Improvement of Interstitial Lung Disease Following Enzyme Replacement Therapy with Olipudase Alfa in Children and Adults with Chronic Acid Sphingomyelinase Deficiency

D98. TARGETING THE SCAR: MECHANISMS AND TREATMENTS FOR FIBROTIC LUNG DISEASE, 2022
Berger, K.I., Scarpa, M., Diaz, G.A., Giugliani, R., Lachmann, R., Wasserstein, M.P., Bonella, Francesco, Walsh, S.L.F., Wuyts, W.A., Jessel, A., Rawlings, A.M., Kumar, M.   +11 more
openaire   +1 more source

Olipudase alfa

Reactions Weekly
openaire   +1 more source

Successful omalizumab use after failed desensitization in olipudase alfa-induced anaphylaxis

Molecular Genetics and Metabolism
Carolina S. Aranda, Sandra Kyosen, Ana Maria Martins   +2 more
openaire   +1 more source

Elastoresonance as a surveillance tool in a patient with acid sphingomyelinase deficiency undergoing treatment with olipudase alfa

Molecular Genetics and Metabolism
Magdalena Ceron-Rodriguez, Carlos P. Acosta Rodríguez Bueno, Judith Almanza-Aranda, Alan E. Araujo Carrillo, Karla Cifuentes-Uribe   +4 more
openaire   +1 more source

Case report: Treatment of the severe ASMD phenotype with olipudase alfa and JZP-150

Molecular Genetics and Metabolism
Justin Hopkin, Steven Laffoon, Joy Chen, Sophia Abner   +3 more
openaire   +1 more source

Novel first-dose adverse drug reactions during a phase I trial of olipudase alfa (recombinant human acid sphingomyelinase) in adults with Niemann–Pick disease type B (acid sphingomyelinase deficiency)

Genetics in Medicine, 2016
Melissa P Wasserstein, Gerald F Cox, Beth L Thurberg   +2 more
exaly  

Olipudase alfa in adult and pediatric ASMD patients: Interim results from French early access program

Molecular Genetics and Metabolism
Nathalie Guffon, Nadia Belmatoug, Nihal Martis, Christian Lavigne, Karin Mazodier, Achille Aouba, Anne Christophe, Olivier Lidove   +7 more
openaire   +1 more source

Efficacy and Safety of Olipudase Alfa for the Treatment of Acid Sphingomyelinase Deficiency (ASMD): A Systematic Review and Meta-Analysis

American Journal of Medical Genetics, Part A
Paulo Victor Zattar Ribeiro, Giovanna Giovacchini dos Santos, Anna Luiza Braga Albuquerque   +2 more
exaly  

Olipudase alfa (Mangel an saurer Sphingomyelinase); Nutzenbewertung gemäß § 35a SGB V

openaire   +1 more source