Results 181 to 190 of about 3,107 (205)
Some of the next articles are maybe not open access.
Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial.
Nature MedicineCrystal M Proud, D. Vũ, J. Wilmshurst, O. Sanmaneechai, S. Gulati, H. Xiong, H. C. Moreno, S. Tay, M. Thong, A. Born, Adriana Banzzatto Ortega, Y. Jong, M. Al-muhaizea, Anna W Lee, J. Visootsak, S. Tauscher‐Wisniewski, Iulian Alecu, R. Parlikar, Richard S. Finkel +18 moresemanticscholar +1 more sourcePilocytic Astrocytoma in a Child with Spinal Muscular Atrophy Treated with Onasemnogene Abeparvovec.
Molecular TherapyD. Holzwarth, G. Calaminus, Johannes Friese, T. Sejersen, Hildegard Büning, Philipp John-Neek, Antonella L. Bastone, Michael Rothe, Keith Mansfield, S. Libertini, Valerie Dubost, Brent J Kuzmiski, I. Alecu, Ivan Labik, Jan Kirschner +14 moresemanticscholar +1 more source