Results 201 to 205 of about 3,107 (205)
Some of the next articles are maybe not open access.
410PIntrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: phase 3b, open-label STRENGTH study
Neuromuscular DisordersJ. Kwon, F. Munell, L. L. Goff, K. Yuge, T. Kato, C. Cances, L. De Waele, I. Woodcock, E. Mercuri, C. Proud, B. Darras, L. Hayes, M. Oskoui, J. Visootsak, G. Williams, A. Lee, A. Ilić, L. Yang, W. van der Pol +18 moresemanticscholar +1 more source588PExpert consensus on gene therapy for spinal muscular atrophy with onasemnogene abeparvovec: treatment decision, administration and patient follow-up
Neuromuscular DisordersJ. Davion, I. Desguerre, F. Audic, C. Cances, C. Barnérias, C. Espil-Taris, B. Fauroux, Y. de Feraudy, M. Guichard, A. Isapof, S. Q. Roy, C. Vuillerot, E. Bodiguel +12 moresemanticscholar +1 more source
