Results 211 to 220 of about 967,148 (255)

Onasemnogene Abeparvovec in Patients With SMA: Interim Results of the RESTORE Registry in Japan

Annals of Clinical and Translational Neurology, EarlyView.
ABSTRACT Objective There are limited real‐world data regarding the safety and effectiveness of onasemnogene abeparvovec (OA; Zolgensma) infusion, a one‐time gene replacement therapy, for Japanese patients with spinal muscular atrophy (SMA). We aimed to improve understanding of the real‐world outcomes for OA in Japan.
Kayoko Saito, Kamal Benguerba, Ken Tsuchida, Kazushige Yazawa, Isao Tsumiyama, Hiromitsu Kayama, Sandra P. Reyna, Farid Khan, Richard S. Finkel   +8 more
wiley   +1 more source

Late-Onset Third Degree Atrioventricular Block in Adult With Surgically Corrected Ebstein Anomaly: A Case Report. [PDF]

Clin Case Rep
Yadav BK, Sigdel B, Mandal B, Mahato A, Basnet B, Yadav S, Bhattarai A.   +6 more
europepmc   +1 more source

Cervical vertebral body metastasis from a gonadotroph pituitary neuroendocrine tumor: illustrative case. [PDF]

J Neurosurg Case Lessons
Song C, Lee J, Shin HC, Oh JK, Hong JB, Yoon HG.   +5 more
europepmc   +1 more source

The underestimated global burden and projections of early-onset stomach and early-onset esophageal cancers. [PDF]

J Gastrointest Oncol
Pustake M.
europepmc   +1 more source

Hemophagocytic lymphohistiocytosis poses a substantial socio-economic burden in China. [PDF]

Chin Med J (Engl)
Li M, Cao J, Liu H, He H, Wang J, Wang Z.   +5 more
europepmc   +1 more source

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Electroclinical characterization and classification of symptomatic epilepsies with very early onset by multiple correspondence analysis

Epilepsy Research, 2010
To characterize very early onset symptomatic epilepsies electroclinically, to identify meaningful factors to delineate epilepsy syndromes under this category, and to test validity of the current syndromic organization of these epilepsies by the International League Against Epilepsy (ILAE).Subjects were 38 epileptic patients with seizure onset before 3 ...
Tomoyuki Akiyama
exaly   +3 more sources

Correspondence. Abrupt onset of severe Behcet's disease: preceding oral ulceration is not essential for diagnosis

British Journal of Dermatology, 1998
Ko-Ron Chen
exaly   +2 more sources